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1 . Academic Journal
CRISPR-Cas9 correction of a nonsense mutation in LCA5 rescues lebercilin expression and localization in human retinal organoids
저자
by
Tess A.V. Afanasyeva
;
Dimitra Athanasiou
;
Pedro R.L. Perdigao
;
Kae R. Whiting
;
Lonneke Duijkers
, et al.
소스
Molecular Therapy: Methods & Clinical Development, Vol 29, Iss , Pp 522-531 (2023)
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7 . Academic Journal
AAV8BP2 and AAV8 transduce the mammalian cochlear lateral wall and endolymphatic sac with high efficiency
저자
by
Kevin Isgrig
;
Yasuko Ishibashi
;
Hyun Jae Lee
;
Jianliang Zhu
;
Mhamed Grati
, et al.
소스
Molecular Therapy: Methods & Clinical Development, Vol 26, Iss , Pp 371-383 (2022)
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7 . Academic Journal
Dynamic structural remodeling of the human visual system prompted by bilateral retinal gene therapy
저자
by
Manzar Ashtari
;
Philip Cook
;
Mikhail Lipin
;
Yinxi Yu
;
Gui-Shuang Ying
, et al.
소스
Current Research in Neurobiology, Vol 4, Iss , Pp 100089- (2023)
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7 . Academic Journal
Motion-selective areas V5/MT and MST appear resistant to deterioration in choroideremia
저자
by
Edward H. Silson
;
Chris I. Baker
;
Tomas S. Aleman
;
Albert M. Maguire
;
Jean Bennett
, et al.
소스
NeuroImage: Clinical, Vol 38, Iss , Pp 103384- (2023)
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7 . Academic Journal
AAV-mediated PEX1 gene augmentation improves visual function in the PEX1-Gly844Asp mouse model for mild Zellweger spectrum disorder
저자
by
Catherine Argyriou
;
Anna Polosa
;
Ji Yun Song
;
Samy Omri
;
Bradford Steele
, et al.
소스
Molecular Therapy: Methods & Clinical Development, Vol 23, Iss , Pp 225-240 (2021)
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7 . Academic Journal
Refining surgical techniques for efficient posterior semicircular canal gene delivery in the adult mammalian inner ear with minimal hearing loss
저자
by
Jianliang Zhu
;
Jin Woong Choi
;
Yasuko Ishibashi
;
Kevin Isgrig
;
Mhamed Grati
, et al.
소스
Scientific Reports, Vol 11, Iss 1, Pp 1-10 (2021)
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7 . Academic Journal
Safety of Same-Eye Subretinal Sequential Readministration of AAV2-hRPE65v2 in Non-human Primates
저자
by
Lindsey Weed
;
Michael J. Ammar
;
Shangzhen Zhou
;
Zhangyong Wei
;
Leona W. Serrano
, et al.
소스
Molecular Therapy: Methods & Clinical Development, Vol 15, Iss , Pp 133-148 (2019)
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7 . Academic Journal
Improving the Quantification of the Lateral Geniculate Nucleus in Magnetic Resonance Imaging Using a Novel 3D-Edge Enhancement Technique
저자
by
Mikhail Lipin
;
Jean Bennett
;
Gui-Shuang Ying
;
Yinxi Yu
;
Manzar Ashtari
.
소스
Frontiers in Computational Neuroscience, Vol 15 (2021)
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7 . Academic Journal
AAV2.7m8 is a powerful viral vector for inner ear gene therapy
저자
by
Kevin Isgrig
;
Devin S. McDougald
;
Jianliang Zhu
;
Hong Jun Wang
;
Jean Bennett
, et al.
소스
Nature Communications, Vol 10, Iss 1, Pp 1-8 (2019)
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7 . Academic Journal
Compensatory Cross-Modal Plasticity Persists After Sight Restoration
저자
by
Theresa G. Mowad
;
Aimee E. Willett
;
Mani Mahmoudian
;
Mikhail Lipin
;
Armin Heinecke
, et al.
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Frontiers in Neuroscience, Vol 14 (2020)
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