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1 . Academic Journal
Diagnostic evaluation of paediatric autoimmune lymphoproliferative immunodeficiencies (ALPID): a prospective cohort study
저자
by
Abinun, Mario
;
Abrahamsen, Tore G.
;
Albert, Michael H.
;
Almalky, Mohamed
;
Altaf, Sadaf
, et al.
소스
In
The Lancet Haematology
February 2024 11(2):e114-e126
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7 . Academic Journal
T-cell replete cord transplants give superior outcomes in high-risk and relapsed/refractory pediatric myeloid malignancy
저자
by
Horgan, Claire
;
Mullanfiroze, Khushnuma
;
Rauthan, Archana
;
Patrick, Katharine
;
Butt, Naeem Akram
, et al.
소스
In
Blood Advances
23 May 2023 7(10):2155-2165
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7 . Academic Journal
Alemtuzumab, Dual Graft-versus-Host Disease Prophylaxis, and Lower CD3+ T Cell Doses Equalize Rates of Acute and Chronic Graft-versus-Host Disease in Pediatric Patients Receiving Allogeneic Hematopoietic Stem Cell Transplantation with Matched Unrelated Donor Peripheral Blood Stem Cells or Bone Marrow Grafts
저자
by
Lum, Su Han
;
James, Beki
;
Ottaviano, Giorgio
;
Ewins, Anna-Maria
;
Patrick, Katharine
, et al.
소스
In
Transplantation and Cellular Therapy
March 2024 30(3):314-314
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7 . Academic Journal
A comprehensive targeted next‐generation sequencing panel for genetic diagnosis of patients with suspected inherited thrombocytopenia
저자
by
Johnson, Ben
;
Doak, Rachel
;
Allsup, David
;
Astwood, Emma
;
Evans, Gillian
, et al.
소스
In
Research and Practice in Thrombosis and Haemostasis
October 2018 2(4):640-652
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7 . Academic Journal
HLA‐haploidentical stem cell transplantation in children with inherited bone marrow failure syndromes: A retrospective analysis on behalf of EBMT severe aplastic Anemia and pediatric diseases working parties.
저자
by
Giardino, Stefano
;
Eikema, Dirk‐Jan
;
Piepenbroek, Brian
;
Algeri, Mattia
;
Ayas, Mouhab
, et al.
소스
American Journal of Hematology; Jun2024, Vol. 99 Issue 6, p1066-1076, 11p
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7 . Academic Journal
Haemopoietic stem cell transplantation is a curative treatment option with minimal transplant-related complications for patients with severe Glanzmann's thrombasthenia
저자
by
Crone, Charlotte
;
James, Beki
.
소스
In
Clinical Medicine
March 2019 19(2) Supplement:s34-s34
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4 . Academic Journal
HLA-Haploidentical Stem Cell Transplantation in Children with Inherited Bone Marrow Failure Syndromes: A Retrospective Analysis on Behalf of EBMT Severe Aplastic Anemia Working Party
저자
by
Giardino, Stefano
;
Eikema, Dirk-Jan
;
Piepenbroek, Brian
;
Algeri, Mattia
;
Ayas, Mouhab
, et al.
소스
In
Blood
15 November 2022 140 Supplement 1:5813-5815
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7 . Academic Journal
T-Cell Replete Unrelated Cord Blood Transplant Give Superior Outcomes to Other Donor Sources in High Risk and Relapsed/Refractory Paediatric Myeloid Malignancy
저자
by
Horgan, Claire
;
Mullanfiroze, Khushnuma
;
Rauthan, Archana
;
Patrick, Katharine
;
Butt, Naeem Akram
, et al.
소스
In
Blood
15 November 2022 140 Supplement 1:4889-4891
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7 . Periodical
Diagnostic evaluation of paediatric autoimmune lymphoproliferative immunodeficiencies (ALPID): a prospective cohort study
저자
by
Hägele, Pauline
;
Staus, Paulina
;
Scheible, Raphael
;
Uhlmann, Annette
;
Heeg, Maximilian
, et al.
소스
The Lancet Haematology; February 2024, Vol. 11 Issue: 2 pe114-e126, 13p
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7 . Academic Journal
Rare missense variants in Tropomyosin‐4 (TPM4) are associated with platelet dysfunction, cytoskeletal defects, and excessive bleeding
저자
by
Stapley, Rachel J.
;
Poulter, Natalie S.
;
Khan, Abdullah O.
;
Smith, Christopher W.
;
Bignell, Patricia
, et al.
소스
In
Journal of Thrombosis and Haemostasis
February 2022 20(2):478-485
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