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1 . Academic Journal
Scavenger receptor class B type I is solely responsible for the selective uptake of cholesteryl esters from HDL by the liver and the adrenals in mice
저자
by
Ruud Out
;
Menno Hoekstra
;
John A.A. Spijkers
;
Johan K. Kruijt
;
Miranda van Eck
, et al.
소스
Journal of Lipid Research, Vol 45, Iss 11, Pp 2088-2095 (2004)
Full Text (ScienceDirect)
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7 . Academic Journal
Effect of Adeno-Associated Virus Serotype and Genomic Structure on Liver Transduction and Biodistribution in Mice of Both Genders.
저자
by
Astrid Pañeda
;
Lucia Vanrell
;
Itsaso Mauleon
;
Julien S. Crettaz
;
Pedro Berraondo
, et al.
소스
Human Gene Therapy
. Aug2009, Vol. 20 Issue 8, p908-917. 10p.
Web of Science
Scopus
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7 . Academic Journal
Correction of Feline Lipoprotein Lipase Deficiency with Adeno-Associated Virus Serotype 1-Mediated Gene Transfer of the Lipoprotein Lipase S447X Beneficial Mutation.
저자
by
Colin J.D. Ross
;
Jaap Twisk
;
Andrew C. Bakker
;
Fudan Miao
;
Dennis Verbart
, et al.
소스
Human Gene Therapy; May2006, Vol. 17 Issue 5, p487-499, 13p
Web of Science
Scopus
JCR 저널정보
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7 . Academic Journal
Gene Therapy for Lipoprotein Lipase Deficiency:Working Toward Clinical Application.
저자
by
Jaap Rip
;
Melchior C. Nierman
;
Jeroen A. Sierts
;
Wilma Petersen
;
Karin Van Den Oever
, et al.
소스
Human Gene Therapy; Nov2005, Vol. 16 Issue 11, p1276-1286, 11p
Web of Science
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7 . Academic Journal
Long-Term Correction of Murine Lipoprotein Lipase Deficiency with AAV1-Mediated Gene Transfer of the Naturally Occurring LPLS447X Beneficial Mutation.
저자
by
Colin J.D. Ross
;
Jaap Twisk
;
Janneke M. Meulenberg
;
Guoqing Liu
;
Karin Van Den Oever
, et al.
소스
Human Gene Therapy; Sep2004, Vol. 15 Issue 9, p906-919, 14p
Web of Science
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7 .
Phase I open label liver-directed gene therapy clinical trial for acute intermittent porphyria
저자
by
Antonio Fontanellas
;
Rafael Enríquez de Salamanca
;
Alberto Benito
;
Irene Gil-Farina
;
Harald Petry
, et al.
소스
Journal of Hepatology
. 65(4):776-783
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7 .
Clearance of Vector DNA Following Systemic Administration of AAV5-hFIX or AAV5-hFIX Padua in Patients with Severe or Moderate-Severe Hemophilia B
저자
by
Jaap Twisk
;
Robert Gut
;
Sander Gielen
;
Alison Long
;
Eileen K. Sawyer
.
소스
Blood
. 134:2062-2062
Open Access (OpenAIRE)
Full Text (ScienceDirect O/A)
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7 .
Immune responses to intramuscular administration of alipogene tiparvovec (AAV1-LPL(S447X)) in a phase II clinical trial of lipoprotein lipase deficiency gene therapy
저자
by
Eleonora Aronica
;
Julie Méthot
;
Valerie Ferreira
;
Harald Petry
;
Karin L. Kwikkers
, et al.
소스
Human gene therapy, 25(3), 180-188. Mary Ann Liebert Inc.
Open Access (OpenAIRE)
Web of Science
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7 .
Efficacy and long term safety of alipogene tiparvovec (AAV1-LPLS447X) gene therapy for lipoprotein lipase deficiency: an open label trial
저자
by
J. de Wal
;
Julie Méthot
;
C Essiembre
;
V Sier-Ferreira
;
Daniel Gaudet
, et al.
소스
Gene therapy
Open Access (OpenAIRE)
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7 .
Effect of Alipogene Tiparvovec (AAV1-LPLS447X) on Postprandial Chylomicron Metabolism in Lipoprotein Lipase-Deficient Patients
저자
by
Frédérique Frisch
;
Janneke de Wal
;
André C. Carpentier
;
René Gagnon
;
Sébastien M. Labbé
, et al.
소스
The Journal of Clinical Endocrinology & Metabolism
. 97:1635-1644
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