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1 .
EE471 Cost Effectiveness of Newborn Screening (NBS) for Spinal Muscular Atrophy (SMA) in England
저자
by
D Weidlich
;
L Servais
;
I Kausar
;
R Howells
;
M Bischof
.
소스
Value in Health
. 25:S148
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7 .
S11 Long-term follow-up of the phase 1 START trial of onasemnogene abeparvovec gene therapy in spinal muscular atrophy type 1
저자
by
N. Miller
;
M Meriggioli
;
Lindsay N. Alfano
;
Samiah Al-Zaidy
;
I Kausar
, et al.
소스
Predicting longer term outcomes in children
.
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7 .
S12 Onasemnogene abeparvovec gene therapy for spinal muscular atrophy type 1: phase 3 study (STR1VE-US)
저자
by
Sitra Tauscher-Wisniewski
;
Thomas O. Crawford
;
Susan T. Iannaccone
;
Claudia A. Chiriboga
;
Basil T. Darras
, et al.
소스
Predicting longer term outcomes in children
.
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7 .
P37 Onasemnogene abeparvovec gene-replacement therapy for spinal muscular atrophy: from bench to bedside
저자
by
Brian K. Kaspar
;
P Kaufmann
;
KD Foust
;
A Kaspar
;
Jerry R. Mendell
, et al.
소스
Ventilation in neuromuscular disease
.
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7 .
S61 Onasemnogene abeparvovec gene-replacement therapy (GRT) for spinal muscular atrophy type 1 (SMA1): preliminary pulmonary and ventilatory findings from the phase 3 study (STR1VE)
저자
by
Richard S. Finkel
;
Nancy L. Kuntz
;
John W. Day
;
Perry B. Shieh
;
Anne M. Connolly
, et al.
소스
Diagnostic and therapeutic advances in paediatrics
.
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7 .
S10 Cost Burden Of N-acetylcysteine (nac) In Adult Patients With Idiopathic Pulmonary Fibrosis
저자
by
I Kausar
;
N Chaudhuri
;
R Nasr
.
소스
Thorax
. 69:A8-A8
Full Text (BMJ Journals)
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5 .
P18 Idiopathic pulmonary fibrosis survival has not improved in the 21st century; analysis of CPRD gold primary care data
저자
by
R Boggon
;
Tm Maher
;
I Kausar
;
H Strongman
.
소스
Thorax
. 68:A82.2-A83
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6 .
P127 Prevalence and Incidence of Idiopathic Pulmonary Fibrosis in UK Healthcare Databases, GPRD and THIN; The Need For an IPF Registry
저자
by
R Cameron
;
F Bugnard
;
C Giot
;
Paula L Thompson
;
WC Maier
, et al.
소스
Thorax
. 67:A117.1-A117
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7 .
P129 Patient and Physician Demographics in Idiopathic Pulmonary Fibrosis: Results of a UK Physician Survey
저자
by
R Cameron
;
I Kausar
;
NC Eastmond
.
소스
Thorax
. 67:A118.1-A118
Full Text (BMJ Journals)
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5 .
P128 Practise Patterns in Idiopathic Pulmonary Fibrosis: Results of a UK Physician Survey
저자
by
NC Eastmond
;
R Cameron
;
I Kausar
.
소스
Thorax
. 67:A117.2-A118
Full Text (BMJ Journals)
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