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1 . Academic Journal
Spk-9001: Adeno-Associated Virus Mediated Gene Transfer for Hemophilia B Achieves Sustained Factor IX with Minimal Immune Response
저자
by
Hui, Daniel J
;
Liu, Yun
;
Patel, Ruchi
;
Chen, Yifeng
;
George, Lindsey A.
, et al.
소스
In
Blood
8 December 2017 130 Supplement 1:2056-2056
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7 . Academic Journal
Spk-8011: Preliminary Results from a Phase 1/2 Dose Escalation Trial of an Investigational AAV-Mediated Gene Therapy for Hemophilia a
저자
by
George, Lindsey A.
;
Ragni, Margaret V.
;
Samelson-Jones, Ben J.
;
Cuker, Adam
;
Runoski, Alexa R.
, et al.
소스
In
Blood
8 December 2017 130 Supplement 1:604-604
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7 . Academic Journal
Immunosuppression Modulates Immune Responses to AAV Capsid in Human Subjects Undergoing Intramuscular Gene Transfer for Lipoprotein Lipase Deficiency
저자
by
Hui, Daniel J
;
Mingozzi, Federico
;
Kleefstra, Annemarie
;
Meulenberg, Janneke M
;
Edmonson, Shyrie
, et al.
소스
In
Blood
16 November 2008 112(11):822-822
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7 . Periodical
A Phase 1/2 Trial of Investigational Spk-8011 in Hemophilia a Demonstrates Durable Expression and Prevention of Bleeds
저자
by
High, Katherine A.
;
George, Lindsey A.
;
Eyster, M. Elaine
;
Sullivan, Spencer K.
;
Ragni, Margaret V.
, et al.
소스
Blood; November 2018, Vol. 132 Issue: Supplement 1 p487-487, 1p
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7 . Academic Journal
Modulation of CD8
+
T cell responses to AAV vectors with IgG-derived MHC class II epitopes.
저자
by
Hui, Daniel J
;
Basner-Tschakarjan, Etiena
;
Chen, Yifeng
;
Davidson, Robert J
;
Buchlis, George
, et al.
소스
Molecular Therapy
. Sep2013, Vol. 21 Issue 9, p1. 1p.
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7 . Periodical
Proteasome Inhibitors Decrease AAV2 Capsid-Derived Peptide Epitope Presentation On MHC Class I Following Transduction.
저자
by
Finn, Jonathan D
;
Hui, Daniel J
;
Harre, Downey
;
Dunn, Danielle
;
Mingozzi, Federico
, et al.
소스
Blood; November 2009, Vol. 114 Issue: 22 p695-695, 1p
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7 . Periodical
Suppression of CTL Responses against AAV-Capsid Epitopes by Peptide-Induced Regulatory T Cells.
저자
by
Hui, Daniel J
;
Pien, Gary C
;
Basner-Tschakarjan, Etiena
;
Mingozzi, Federico
;
Finn, Jonathan D
, et al.
소스
Blood; November 2009, Vol. 114 Issue: 22 p377-377, 1p
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