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1 . Academic Journal
Visualizing Muscle Sialic Acid Expression in the GNE
D207V
Tg
Gne
-/-
Cmah
-/-
Model of GNE Myopathy: A Comparison of Dietary and Gene Therapy Approaches.
저자
by
Crowe, Kelly E.
;
Zygmunt, Deborah A.
;
Heller, Kristin
;
Rodino-Klapac, Louise
;
Noguchi, Satoru
, et al.
소스
Journal of Neuromuscular Diseases; 2022, Vol. 9 Issue 1, p53-71, 19p
Web of Science
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7 . Periodical
Visualizing Muscle Sialic Acid Expression in the GNED207VTgGne-/-Cmah-/-Model of GNE Myopathy: A Comparison of Dietary and Gene Therapy Approaches
저자
by
Crowe, Kelly E.
;
Zygmunt, Deborah A.
;
Heller, Kristin
;
Rodino-Klapac, Louise
;
Noguchi, Satoru
, et al.
소스
Journal of Neuromuscular Diseases; January 2022, Vol. 9 Issue: 1 p53-71, 19p
Web of Science
Scopus
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7 . Academic Journal
Micro-dystrophin and follistatin co-delivery restores muscle function in aged DMD model
저자
by
Rodino-Klapac, Louise R.
;
Janssen, Paul M. L.
;
Shontz, Kimberly M.
;
Canan, Benjamin
;
Montgomery, Chrystal L.
, et al.
소스
Human Molecular Genetics
. Dec 15, 2013 22(24):4929-4937
Full Text (OUP)
Full Text (OUP Near Archive)
Web of Science
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7 . Academic Journal
mRNA expression of genes involved in fatty acid utilization in skeletal muscle and white adipose tissues of sows during lactation
저자
by
Ringseis, Robert
;
Heller, Kristin
;
Kluge, Holger
;
Eder, Klaus
.
소스
Comparative Biochemistry & Physiology Part A: Molecular & Integrative Physiology
. Apr2011, Vol. 158 Issue 4, p450-454. 5p.
Full Text (ScienceDirect)
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6 . Academic Journal
Identification of M-tuberculosis Thioredoxin Reductase Inhibitors Based on High-Throughput Docking Using Constraints
저자
by
Koch, Oliver
;
Jaeger, Timo
;
Heller, Kristin
;
Khandavalli, Purushothama Chary
;
Pretzel, Jette
, et al.
소스
JOURNAL OF MEDICINAL CHEMISTRY
; JUN 27 2013, 56 12, p4849-p4859, 11p.
Full Text (ACS)
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7 . Academic Journal
Systemic Gene Therapy Restores gamma-Sarcoglycan Expression in Skeletal and Cardiac Muscle in LGMD2C Mice
저자
by
Pozsgai, Eric
;
Griffin, Danielle
;
Heller, Kristin
;
Mendell, Jerry
;
Rodino-Klapac, Louise
.
소스
MOLECULAR THERAPY
; MAY 2018, 26 5, p119-p120, 2p. Supplement: 1
Full Text (ScienceDirect)
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7 . Academic Journal
Toxicity & Biodistribution Study Demonstrates Safety of AAV-Mediated Human Beta-Sarcoglycan Gene Therapy
저자
by
Pozsgai, Eric
;
Griffin, Danielle
;
Heller, Kristin
;
Mendell, Jerry
;
Rodino-Klapac, Louise
.
소스
MOLECULAR THERAPY
; MAY 2017, 25 5, p19-p20, 2p. Supplement: 1
Full Text (ScienceDirect)
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7 . Academic Journal
Systemic beta-Sarcoglycan Gene Therapy for Treatment of Cardiac and Skeletal Muscle Deficits in LGMD2E
저자
by
Pozsgai, Eric
;
Griffin, Danielle
;
Heller, Kristin
;
Mendell, Jerry
;
Rodino-Klapac, Louise
.
소스
MOLECULAR THERAPY
; MAY 2016, 24 pS246-pS247, 2p. Supplement: 1
Full Text (ScienceDirect O/A)
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7 . Academic Journal
Systemic Dose Escalation Study of Alpha-Sarcoglycan Provides Functional Improvement in SGCA(/-)Mouse Model of LGMD2D
저자
by
Griffin, Danielle
;
Heller, Kristin
;
Shontz, Kim
;
Peterson, Ellyn
;
Pozsgai, Eric
, et al.
소스
MOLECULAR THERAPY
; MAY 2018, 26 5, p166-p166, 1p. Supplement: 1
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7 . Academic Journal
Prolonged Exon 2 Skipping and Robust Dystrophin Expression 1 Year Post Single Neonatal Injection of an AAV9. U7snRNA Vector in the Dup2 Mouse
저자
by
Wein, Nicolas
;
Simmons, Tabatha
;
Gumienny, Felecia
;
Huang, Nianyuan
;
Heller, Kristin
, et al.
소스
MOLECULAR THERAPY
; MAY 2017, 25 5, p19-p19, 1p. Supplement: 1
Full Text (ScienceDirect)
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