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1 . Academic Journal
Patientenpartizipation in der pädiatrischen Versorgungsforschung am Universitätsklinikum Freiburg: von der Projektbeteiligung zum Patientenbeirat
저자
by
Langer, Thorsten
;
Gusset, Nicole
;
Pechmann, Astrid
;
Stumpe, Eva
;
Dürr, Susanne
, et al.
소스
In
Zeitschrift fuer Evidenz, Fortbildung und Qualitaet im Gesundheitswesen
September 2022 173:98-105
Full Text (ScienceDirect)
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7 . Academic Journal
Understanding European patient expectations towards current therapeutic development in spinal muscular atrophy
저자
by
Gusset, Nicole
;
Stalens, Caroline
;
Stumpe, Eva
;
Klouvi, Lori
;
Mejat, Alexandre
, et al.
소스
In
Neuromuscular Disorders
May 2021 31(5):419-430
Full Text (Clinical Key)
Full Text (ScienceDirect)
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7 . Academic Journal
A Decision for Life – Treatment decisions in newly diagnosed families with spinal muscular atrophy (SMA)
저자
by
Gusset, Nicole
;
Erbas, Yasemin
;
Germanenko, Olga
;
Rucinski, Kacper
;
Stumpe, Eva
, et al.
소스
In
European Journal of Paediatric Neurology
January 2021 30:105-107
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7 . Academic Journal
Disease impact on general well-being and therapeutic expectations of European Type II and Type III spinal muscular atrophy patients
저자
by
Rouault, Françoise
;
Christie-Brown, Vanessa
;
Broekgaarden, Ria
;
Gusset, Nicole
;
Henderson, Doug
, et al.
소스
In
Neuromuscular Disorders
May 2017 27(5):428-438
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7 . Academic Journal
Systematic Literature Review of the Natural History of Spinal Muscular Atrophy: Motor Function, Scoliosis, and Contractures.
저자
by
Ribero, Valerie Aponte
;
Martí, Yasmina
;
Batson, Sarah
;
Mitchell, Stephen
;
Gorni, Ksenija
, et al.
소스
Neurology; 11/21/2023, Vol. 101 Issue 21, pe2103-e2113, 11p
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7 . Conference
254th ENMC international workshop. Formation of a European network to initiate a European data collection, along with development and sharing of treatment guidelines for adult SMA patients. Virtual meeting 28 – 30 January 2022
저자
by
Attarian, Shahram
;
Bartels, Bart
;
Gorni, Ksenija
;
Goemans, Nathalie
;
Gusset, Nicole
, et al.
소스
In
Neuromuscular Disorders
June 2023 33(6):511-522
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7 . Academic Journal
Reverse Engineering of Digital Measures: Inviting Patients to the Conversation.
저자
by
Clay, Ieuan
;
Peerenboom, Nele
;
Connors, Dana E
;
Bourke, Steven
;
Keogh, Alison
, et al.
소스
Digital Biomarkers; 2023, Vol. 7 Issue 1, p28-44, 17p
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7 . Academic Journal
Importance of Patient Involvement in the Value Assessment Process: On the Way Towards Personalised Treatments.
저자
by
Gusset, Nicole
.
소스
PharmacoEconomics
. Apr2022 Supplement 1, Vol. 40 Issue 1, p7-10. 4p.
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3 . Academic Journal
A Patient-Centered Evaluation of Meaningful Change on the 32-Item Motor Function Measure in Spinal Muscular Atrophy Using Qualitative and Quantitative Data.
저자
by
Duong, Tina
;
Staunton, Hannah
;
Braid, Jessica
;
Barriere, Aurelie
;
Trzaskoma, Ben
, et al.
소스
Frontiers in Neurology; 1/17/2022, p1-12, 12p
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7 . Academic Journal
Understanding the relationship between the 32-item motor function measure and daily activities from an individual with spinal muscular atrophy and their caregivers' perspective: a two-part study.
저자
by
Duong, Tina
;
Braid, Jessica
;
Staunton, Hannah
;
Barriere, Aurelie
;
Petridis, Fani
, et al.
소스
BMC Neurology
. 9/13/2021, Vol. 21 Issue 1, p1-14. 14p.
Open Access (BioMed Central)
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