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1 . Academic Journal
Small fiber neuropathy in children, adolescents, and young adults with chronic orthostatic intolerance and postural orthostatic tachycardia syndrome: A retrospective study
저자
by
Moak, Jeffrey P.
;
Ramwell, Carolyn B.
;
Gordish-Dressman, Heather
;
Sule, Sangeeta D.
;
Bettini, Elizabeth
.
소스
In
Autonomic Neuroscience: Basic and Clinical
June 2024 253
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7 . Academic Journal
Voluntary wheel running improves molecular and functional deficits in a murine model of facioscapulohumeral muscular dystrophy
저자
by
Bittel, Adam J.
;
Bittel, Daniel C.
;
Gordish-Dressman, Heather
;
Chen, Yi-Wen
.
소스
In
iScience
19 January 2024 27(1)
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6 . Academic Journal
Effects of gene replacement therapy with resamirigene bilparvovec (AT132) on skeletal muscle pathology in X-linked myotubular myopathy: results from a substudy of the ASPIRO open-label clinical trial
저자
by
Lawlor, Michael W.
;
Schoser, Benedikt
;
Margeta, Marta
;
Sewry, Caroline A.
;
Jones, Karra A.
, et al.
소스
In
eBioMedicine
January 2024 99
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7 . Academic Journal
Major Adverse Dystrophinopathy Events (MADE) score as marker of cumulative morbidity and risk for mortality in boys with Duchenne muscular dystrophy
저자
by
Kaufman, Beth D.
;
Garcia, Ariadna
;
He, Zihuai
;
Tesi-Rocha, Carolina
;
Buu, MyMy
, et al.
소스
In
Progress in Pediatric Cardiology
June 2023 69
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7 . Academic Journal
Expanding the muscle imaging spectrum in dysferlinopathy: description of an outlier population from the classical MRI pattern
저자
by
Llansó, Laura
;
Moore, Ursula
;
Bolano-Diaz, Carla
;
James, Meredith
;
Blamire, Andrew M.
, et al.
소스
In
Neuromuscular Disorders
April 2023 33(4):349-357
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7 . Academic Journal
Pediatric resident education in pediatric cardiology – A needs assessment
저자
by
Hovis, Ian W.
;
Frank, Lowell H.
;
Gordish-Dressman, Heather
;
Spurney, Christopher F.
.
소스
In
Progress in Pediatric Cardiology
March 2023 68
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6 . Academic Journal
Myostatin and follistatin as monitoring and prognostic biomarkers in dysferlinopathy
저자
by
Moore, Ursula
;
Fernández-Simón, Esther
;
Schiava, Marianela
;
Cox, Dan
;
Gordish-Dressman, Heather
, et al.
소스
In
Neuromuscular Disorders
February 2023 33(2):199-207
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7 . Academic Journal
Laminated holmium-166-containing electrospun bandages for use against skin cancer
저자
by
Osipitan, Ositomiwa O.
;
Sun, Mengwei
;
Gordish-Dressman, Heather
;
Wendt, Richard, III
;
Wight-Carter, Mary
, et al.
소스
In
Nuclear Medicine and Biology
November-December 2022 114-115:78-85
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7 . Academic Journal
Complete unroofing of the intramural coronary artery for anomalous aortic origin of a coronary artery: The role of commissural resuspension?
저자
by
Yerebakan, Can
;
Ozturk, Mahmut
;
Mota, Lucas
;
Sinha, Lok
;
Gordish-Dressman, Heather
, et al.
소스
In
The Journal of Thoracic and Cardiovascular Surgery
July 2019 158(1):208-217
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7 . Academic Journal
Long-term effects of glucocorticoids on function, quality of life, and survival in patients with Duchenne muscular dystrophy: a prospective cohort study
저자
by
Vishwanathan, Vijay
;
Chidambaranathan, S
;
Biggar, W. Douglas
;
McAdam, Laura C.
;
Mah, Jean K.
, et al.
소스
In
The Lancet
3-9 February 2018 391(10119):451-461
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