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1 . Academic Journal
Novel AAV variants with improved tropism for human Schwann cells
저자
by
Drouyer, Matthieu
;
Chu, Tak-Ho
;
Labit, Elodie
;
Haase, Florencia
;
Navarro, Renina Gale
, et al.
소스
In
Molecular Therapy - Methods & Clinical Development
13 June 2024 32(2)
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7 . Academic Journal
AAV-delivered hepato-adrenal cooperativity in steroidogenesis: Implications for gene therapy for congenital adrenal hyperplasia
저자
by
Graves, Lara E.
;
van Dijk, Eva B.
;
Zhu, Erhua
;
Koyyalamudi, Sundar
;
Wotton, Tiffany
, et al.
소스
In
Molecular Therapy - Methods & Clinical Development
13 June 2024 32(2)
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7 . Academic Journal
Development of CNS tropic AAV1-like variants with reduced liver-targeting following systemic administration in mice
저자
by
Drouyer, Matthieu
;
Merjane, Jessica
;
Nazareth, Deborah
;
Knight, Maddison
;
Scott, Suzanne
, et al.
소스
In
Molecular Therapy
6 March 2024 32(3):818-836
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7 . Academic Journal
Development of new adeno-associated virus capsid variants for targeted gene delivery to human cardiomyocytes
저자
by
Kok, Cindy Y.
;
Tsurusaki, Shinya
;
Cabanes-Creus, Marti
;
Igoor, Sindhu
;
Rao, Renuka
, et al.
소스
In
Molecular Therapy - Methods & Clinical Development
14 September 2023 30:459-473
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7 . Academic Journal
Efficient in vivo editing of OTC-deficient patient-derived primary human hepatocytes
저자
by
Ginn, Samantha L.
;
Amaya, Anais K.
;
Liao, Sophia H.Y.
;
Zhu, Erhua
;
Cunningham, Sharon C.
, et al.
소스
In
JHEP Reports
February 2020 2(1)
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7 . Academic Journal
Restoring the natural tropism of AAV2 vectors for human liver.
저자
by
Cabanes-Creus, Marti
;
Hallwirth, Claus V.
;
Westhaus, Adrian
;
Ng, Boaz H.
;
Liao, Sophia H.Y.
, et al.
소스
Science Translational Medicine; 9/9/2020, Vol. 12 Issue 560, p1-12, 12p
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7 . Academic Journal
Bone Marrow Transplantation for Treatment of the Col1a2
+/G610C
Osteogenesis Imperfecta Mouse Model.
저자
by
Lee, Lucinda R.
;
Peacock, Lauren
;
Ginn, Samantha L.
;
Cantrill, Laurence C.
;
Cheng, Tegan L.
, et al.
소스
Calcified Tissue International
. Apr2019, Vol. 104 Issue 4, p426-436. 11p.
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7 . Academic Journal
Thymocyte self-renewal and oncogenic risk in immunodeficient mouse models: relevance for human gene therapy clinical trials targeting haematopoietic stem cell populations?
저자
by
Ginn, Samantha L.
;
McCormack, Matthew P.
;
Alexander, Ian E.
.
소스
Mammalian Genome
. Dec2018, Vol. 29 Issue 11/12, p771-776. 6p.
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5 . Academic Journal
Gene therapy clinical trials worldwide to 2017: An update.
저자
by
Ginn, Samantha L.
;
Amaya, Anais K.
;
Alexander, Ian E.
;
Edelstein, Michael
;
Abedi, Mohammad R.
.
소스
Journal of Gene Medicine; May2018, Vol. 20 Issue 5, p1-1, 16p
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7 . Academic Journal
Bone Marrow Transplantation for Treatment of the Col1a2
+/G610C
Osteogenesis Imperfecta Mouse Model
저자
by
Lee, Lucinda R.
;
Peacock, Lauren
;
Ginn, Samantha L.
;
Cantrill, Laurence C.
;
Cheng, Tegan L.
, et al.
소스
Calcified Tissue International: and Musculoskeletal Research
. 104(4):426-436
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