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1 . Academic Journal
Targeting the 5′ untranslated region of SMN2 as a therapeutic strategy for spinal muscular atrophy
저자
by
Audrey M. Winkelsas
;
Christopher Grunseich
;
George G. Harmison
;
Katarzyna Chwalenia
;
Carlo Rinaldi
, et al.
소스
Molecular Therapy: Nucleic Acids, Vol 23, Iss , Pp 731-742 (2021)
Full Text (ScienceDirect)
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7 . Academic Journal
Stem cell-derived motor neurons from spinal and bulbar muscular atrophy patients
저자
by
Christopher Grunseich
;
Kristen Zukosky
;
Ilona R. Kats
;
Laboni Ghosh
;
George G. Harmison
, et al.
소스
Neurobiology of Disease, Vol 70, Iss , Pp 12-20 (2014)
Full Text (Clinical Key)
Full Text (ScienceDirect)
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Web of Science
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7 . Academic Journal
Systemic Delivery of MicroRNA Using Recombinant Adeno-associated Virus Serotype 9 to Treat Neuromuscular Diseases in Rodents
저자
by
Naemeh Pourshafie, author
;
Philip R. Lee, author
;
Ke-lian Chen, author
;
George G. Harmison, author
;
Laura C. Bott, author
, et al.
소스
Journal of Visualized Experiments
. (138)
JoVE Journal
Web of Science
Scopus
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7 .
Targeting the 5' untranslated region of SMN2 as a therapeutic strategy for spinal muscular atrophy
저자
by
Suzan M. Hammond
;
Audrey M. Winkelsas
;
Katarzyna Chwalenia
;
George G. Harmison
;
Carlo Rinaldi
, et al.
소스
Molecular Therapy: Nucleic Acids, Vol 23, Iss, Pp 731-742 (2021)
Molecular Therapy. Nucleic Acids
Open Access (OpenAIRE)
Scopus
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7 .
Systemic Delivery of MicroRNA Using Recombinant Adeno-associated Virus Serotype 9 to Treat Neuromuscular Diseases in Rodents
저자
by
George G. Harmison
;
Naemeh Pourshafie
;
Ke-lian Chen
;
Kenneth H. Fischbeck
;
Philip R. Lee
, et al.
소스
Journal of Visualized Experiments
.
Open Access (OpenAIRE)
Scopus
JCR 저널정보
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RefWorks
7 .
A small-molecule Nrf1 and Nrf2 activator mitigates polyglutamine toxicity in spinal and bulbar muscular atrophy
저자
by
Laura C. Bott
;
J. Paul Taylor
;
Masahisa Katsuno
;
George G. Harmison
;
Nisha M. Badders
, et al.
소스
Human Molecular Genetics
. 25:1979-1989
Full Text (OUP)
Full Text (OUP Near Archive)
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7 .
MiR-298 Counteracts Mutant Androgen Receptor Toxicity in Spinal and Bulbar Muscular Atrophy
저자
by
Carlo Rinaldi
;
Barrington G. Burnett
;
Laura C. Bott
;
Gen Sobue
;
Ke-lian Chen
, et al.
소스
Molecular Therapy
Full Text (ScienceDirect)
Full Text (ScienceDirect O/A)
Open Access (OpenAIRE)
Web of Science
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JCR 저널정보
요약보기
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7 .
Stem cell-derived motor neurons from spinal and bulbar muscular atrophy patients
저자
by
Carlo Rinaldi
;
Manfred Boehm
;
Laura C. Bott
;
Ke-lian Chen
;
Ilona Kats
, et al.
소스
Neurobiology of Disease, Vol 70, Iss, Pp 12-20 (2014)
Full Text (Clinical Key)
Open Access (OpenAIRE)
Web of Science
Scopus
JCR 저널정보
요약보기
Export
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RefWorks
7 .
Genetics of low spinal muscular atrophy carrier frequency in sub‐Saharan Africa
저자
by
Kristen Zukosky
;
Manfred Boehm
;
Andrew B. Singleton
;
Guibin Chen
;
Fatoumata N'Go Yaro
, et al.
소스
Annals of Neurology
Full Text (Wiley)
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Web of Science
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7 .
Mitochondrial abnormalities in spinal and bulbar muscular atrophy
저자
by
George G. Harmison
;
Maria Pennuto
;
Srikanth Ranganathan
;
Kenneth H. Fischbeck
;
Barrington G. Burnett
, et al.
소스
Human Molecular Genetics
Full Text (OUP)
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