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1 . Academic Journal
Cardiac diastolic maladaptation is associated with the severity of exercise intolerance in sickle cell anemia patients
저자
by
Thomas d’Humières
;
Antoine Bouvarel
;
Laurent Boyer
;
Laurent Savale
;
Henri Guillet
, et al.
소스
Scientific Reports, Vol 14, Iss 1, Pp 1-13 (2024)
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7 . Academic Journal
Predictors of health-related quality of life in a large cohort of adult patients living with sickle cell disease in France: the DREPAtient study
저자
by
Issifou Yaya
;
Adrien Pourageaud
;
Benjamin Derbez
;
Marie-Hélène Odièvre
;
Damien Oudin Doglioni
, et al.
소스
Frontiers in Public Health, Vol 12 (2024)
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7 . Academic Journal
Endurance training improves oxygen uptake/demand mismatch, metabolic flexibility and recovery in patients with sickle cell disease
저자
by
Loïs Mougin
;
Manon Riccetti
;
Angèle N. Merlet
;
Pablo Bartolucci
;
Barnabas Gellen
, et al.
소스
Haematologica, Vol 999, Iss 1 (2024)
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7 . Academic Journal
Genetic reversal of the globin switch concurrently modulates both fetal and sickle hemoglobin and reduces red cell sickling
저자
by
Daniel C. De Souza
;
Nicolas Hebert
;
Erica B. Esrick
;
M. Felicia Ciuculescu
;
Natasha M. Archer
, et al.
소스
Nature Communications, Vol 14, Iss 1, Pp 1-10 (2023)
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7 . Academic Journal
Bone mineral density in adult patients with pyruvate kinase deficiency on long-term mitapivat treatment
저자
by
Hanny Al-Samkari
;
Rachael F. Grace
;
Andreas Glenthøj
;
Oliver Andres
;
Wilma Barcellini
, et al.
소스
Haematologica, Vol 109, Iss 3 (2023)
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7 . Academic Journal
Prevalence and cost of sickle cell disease in France: real-world analysis using data from the Echantillon Généraliste des Bénéficiaires
저자
by
Maud Beillat
;
Isabelle Durand-Zaleski
;
France Pirenne
;
Stève Bénard
;
Louis Chillotti
, et al.
소스
Frontiers in Public Health, Vol 11 (2023)
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7 . Academic Journal
P1427: RARE ANAEMIA DISORDERS EUROPEAN EPIDEMIOLOGICAL PLATFORM (RADEEP): DISTRIBUTION OF PATIENTS AFFECTED BY RADS IN EUROPE
저자
by
José Martín Solórzano González
;
Sara Isabel Reidel
;
Ines Labidi
;
Claire Diot Lefebvre
;
Stella Tamana
, et al.
소스
HemaSphere, Vol 7, p e13208ab (2023)
Full Text (LWW)
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7 . Academic Journal
P1473: CLINICALLY RELEVANT HEMOGLOBIN RESPONSE IN ADULTS WITH PYRUVATE KINASE DEFICIENCY TREATED WITH MITAPIVAT – A SUB-ANALYSIS OF THE ACTIVATE TRIAL
저자
by
Hanny Al-Samkari
;
Rachael F. Grace
;
Andreas Glenthøj
;
Wilma Barcellini
;
Madeleine Verhovsek
, et al.
소스
HemaSphere, Vol 7, p e918756f (2023)
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7 . Academic Journal
Psychometric characteristics of the Revised Illness Perception Questionnaire (IPQ-R) in adults with sickle cell disease
저자
by
Damien Oudin Doglioni
;
Anne-Laure Pham-Hung D’Alexandry D’Orengiani
;
Frédéric Galactéros
;
Marie-Claire Gay
.
소스
Health Psychology and Behavioral Medicine, Vol 10, Iss 1, Pp 60-80 (2022)
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6 . Academic Journal
Characterization of genetic variants in the EGLN1/PHD2 gene identified in a European collection of patients with erythrocytosis
저자
by
Marine Delamare
;
Amandine Le Roy
;
Mathilde Pacault
;
Loïc Schmitt
;
Céline Garrec
, et al.
소스
Haematologica, Vol 108, Iss 11 (2023)
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