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1 . Academic Journal
Safety and efficacy of arimoclomol for inclusion body myositis: a multicentre, randomised, double-blind, placebo-controlled trial
저자
by
Dimachkie, Mazen
;
Statland, Jeffrey
;
Pasnoor, Mamatha
;
Jawdat, Omar
;
Heim, Andrew
, et al.
소스
In
The Lancet Neurology
October 2023 22(10):900-911
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7 . Academic Journal
Lean tissue mass measurements by dual-energy X-ray absorptiometry and associations with strength and functional outcome measures in facioscapulohumeral muscular dystrophy
저자
by
Wang, Leo H.
;
Leung, Doris G.
;
Wagner, Kathryn R.
;
Lowry, Sarah J.
;
McDermott, Michael P.
, et al.
소스
In
Neuromuscular Disorders
September 2023 33(9):63-68
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7 . Academic Journal
Antisense oligonucleotide targeting DMPK in patients with myotonic dystrophy type 1: a multicentre, randomised, dose-escalation, placebo-controlled, phase 1/2a trial
저자
by
Thornton, Charles A
;
Moxley, Richard Thomas, III
;
Eichinger, Katy
;
Heatwole, Chad
;
Mignon, Laurence
, et al.
소스
In
The Lancet Neurology
March 2023 22(3):218-228
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7 . Academic Journal
Functional outcome measures in young, steroid-naïve boys with Duchenne muscular dystrophy
저자
by
Mayhew, Anna G
;
Moat, Dionne
;
McDermott, Michael P.
;
Eagle, Michelle
;
Griggs, Robert C.
, et al.
소스
In
Neuromuscular Disorders
June 2022 32(6):460-467
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7 . Academic Journal
A longitudinal study of disease progression in facioscapulohumeral muscular dystrophy (FSHD).
저자
by
Varma, Anika
;
Todinca, Michael S.
;
Eichinger, Katy
;
Heininger, Susanne
;
Dilek, Nuran
, et al.
소스
Muscle & Nerve
. Mar2024, Vol. 69 Issue 3, p362-367. 6p.
Full Text (Wiley)
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7 . Book
10 - Physical therapy for neuromuscular conditions
저자
by
Eichinger, Katy
;
Zablotny, Cynthia
.
소스
In
Introduction to Physical Therapy
Edition: Sixth Edition. 2021:172-189
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4 . Academic Journal
Remote assessment of myotonic dystrophy type 1: A feasibility study.
저자
by
Hamel, Johanna
;
Creigh, Peter D.
;
Dekdebrun, Jeanne
;
Eichinger, Katy
;
Thornton, Charles A.
.
소스
Muscle & Nerve
. Sep2022, Vol. 66 Issue 3, p336-339. 4p.
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7 . Academic Journal
Understanding the Perseverance of the Muscular Dystrophy Community One-Year into the COVID-19 Pandemic.
저자
by
Lewis, Leann
;
Eichinger, Katy
;
Dilek, Nuran
;
Higgs, Kiley
;
Walker, Michaela
, et al.
소스
Journal of Neuromuscular Diseases; 2022, Vol. 9 Issue 4, p517-523, 7p
Web of Science
Scopus
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7 . Academic Journal
Accelerate Clinical Trials in Charcot-Marie-Tooth Disease (ACT-CMT): A Protocol to Address Clinical Trial Readiness in CMT1A.
저자
by
Eichinger, Katy
;
Sowden, Janet E.
;
Burns, Joshua
;
McDermott, Michael P.
;
Krischer, Jeffrey
, et al.
소스
Frontiers in Neurology; 6/27/2022, Vol. 13, p1-10, 10p
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7 . Book
9 - Physical Therapy for Neuromuscular Conditions
저자
by
Eichinger, Katy
;
Zablotny, Cynthia M.
.
소스
In
Introduction to Physical Therapy
Edition: Fifth Edition. 2016:225-249
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