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1 . Academic Journal
Final results of the PUPs B-LONG study: evaluating safety and efficacy of rFIXFc in previously untreated patients with hemophilia B
저자
by
Nolan, Beatrice
;
Klukowska, Anna
;
Shapiro, Amy
;
Rauch, Antoine
;
Recht, Michael
, et al.
소스
In
Blood Advances
13 July 2021 5(13):2732-2739
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7 . Periodical
Safety and Efficacy of Recombinant Fusion Protein Linking Coagulation Factor IX with Albumin (rIX-FP) in Previously Untreated Patients with Hemophilia B
저자
by
Lemons, Richard
;
Wang, Michael
;
Curtin, Julie
;
Lepatan, Lynda Mae
;
Male, Christoph
, et al.
소스
TH Open; January 2024, Vol. 8 Issue: 1 pe155-e163, 9p
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7 . Academic Journal
Immune tolerance induction using a factor VIII/von Willebrand factor concentrate (BIOSTATE®), with or without immunosuppression, in Australian paediatric severe haemophilia A patients with high titre inhibitors: A multicentre, retrospective study
저자
by
Robertson, Jeremy D.
;
Higgins, Pauline
;
Price, Jamie
;
Dunkley, Scott
;
Barrese, Giulio
, et al.
소스
In
Thrombosis Research
November 2014 134(5):1046-1051
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7 . Academic Journal
Pulmonary Embolism in Children
저자
by
Dijk, F. Nicole
;
Curtin, Julie
;
Lord, David
;
Fitzgerald, Dominic A.
.
소스
In
Paediatric Respiratory Reviews
June 2012 13(2):112-122
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6 . Academic Journal
Ultra-rapid genomic testing, a game changer in facilitating disease modifying treatment in a critically ill newborn
저자
by
Balasubramaniam, Shanti
;
Li, Katherine
;
Ma, Alan
;
Lunke, Sebastian
;
Trivedi, Amit
, et al.
소스
In
Pathology
February 2023 55 Supplement 1:S16-S16
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7 . Academic Journal
Biallelic Deleterious Germline SH2B3 Variants Cause a Novel Clinical Syndrome of Myeloproliferation and Multi-Organ Autoimmunity
저자
by
Blombery, Piers
;
Pazhakh, Vahid
;
Albuquerque, Adriana
;
Maimaris, Jesmeen
;
Tu, Lingge
, et al.
소스
In
Blood
15 November 2022 140 Supplement 1:992-993
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7 . Academic Journal
A chameleon in the marrow – one germ cell tumour, two leukaemias
저자
by
Prime, Elizabeth
;
Curtin, Julie
;
Govender, Dinisha
.
소스
In
Pathology
March 2022 54 Supplement 1:S20-S20
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5 . Academic Journal
Allogeneic bone marrow transplantation: cure for familial Mediterranean fever
저자
by
Milledge, John
;
Shaw, Peter J.
;
Mansour, Albert
;
Williamson, Sarah
;
Bennetts, Bruce
, et al.
소스
In
Blood
1 August 2002 100(3):774-777
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7 . Academic Journal
A Practical, One-Clinic Visit Protocol for Pharmacokinetic Profile Generation with the ADVATE myPKFiT Dosing Tool in Severe Hemophilia A Subjects.
저자
by
Blanchette, Victor S.
;
Zunino, Laura
;
Grassmann, Viviane
;
Barnes, Chris
;
Carcao, Manuel D.
, et al.
소스
Thrombosis & Haemostasis; 2021, Vol. 121 Issue 10, p1326-1336, 11p
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7 . Periodical
Newborn screening (NBS) for spinal muscular atrophy: the 5-year New South Wales (NSW) experience of screening 549,000 babies
저자
by
Wotton, Tiffany
;
Kim, Won Tae
;
Junek, Rosie
;
Screening Programme, NSW Newborn
;
Curtin, Julie
, et al.
소스
Pathology; February 2024, Vol. 56 Issue: 1, Number 1 Supplement 1 pS98-S98, 1p
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