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1 . Academic Journal
Preclinical safety and efficacy of lentiviral-mediated gene therapy for leukocyte adhesion deficiency type I
저자
by
Cristina Mesa-Núñez
;
Carlos Damián
;
María Fernández-García
;
Begoña Díez
;
Gayatri Rao
, et al.
소스
Molecular Therapy: Methods & Clinical Development, Vol 26, Iss , Pp 459-470 (2022)
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7 . Academic Journal
The downregulated membrane expression of CD18 in CD34+ cells defines a primitive population of human hematopoietic stem cells
저자
by
Cristina Mesa-Núñez
;
Diego Leon-Rico
;
Montserrat Aldea
;
Carlos Damián
;
Raquel Sanchez-Baltasar
, et al.
소스
Stem Cell Research & Therapy, Vol 11, Iss 1, Pp 1-9 (2020)
Open Access (BioMed Central)
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7 .
Lentiviral-Mediated Ex-Vivo Gene Therapy for Pediatric Patients with Severe Leukocyte Adhesion Deficiency-I (LAD-I): Interim Results from an Ongoing Phase 1/2 Study
저자
by
Claire Booth
;
Julian Sevilla
;
Gayatri Rao
;
Maria Chitty Lopez
;
Elena Almarza
, et al.
소스
Transplantation and Cellular Therapy
. 29:S2-S3
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7 .
Interim Results from an Ongoing Phase 1/2 Study of Lentiviral-mediated Ex-vivo Gene Therapy for Pediatric Patients with Severe Leukocyte Adhesion Deficiency-I (LAD-I)
저자
by
Claire Booth
;
Julián Sevilla
;
Gayatri R. Rao
;
Maria Chitty Lopez
;
Elena Almarza
, et al.
소스
Blood
. 140:7774-7775
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7 .
Preclinical safety and efficacy of lentiviral-mediated gene therapy for leukocyte adhesion deficiency type I
저자
by
Cristina Mesa-Núñez
;
Carlos Damián
;
María Fernández-García
;
Begoña Díez
;
Gayatri Rao
, et al.
소스
Molecular therapy. Methodsclinical development
. 26
Open Access (OpenAIRE)
Scopus
JCR 저널정보
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7 .
A novel genetic variant in PTGS1 affects N-glycosylation of cyclooxygenase-1 causing a dominant-negative effect on platelet function and bleeding diathesis
저자
by
Harriet E. Allan
;
Jesús María Hernández-Rivas
;
Agustín Rodriguez-Alén
;
Elena Almarza
;
Maria Luisa Lozano
, et al.
소스
Digital.CSIC. Repositorio Institucional del CSIC
instname
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7 .
A Phase 1/2 Study of Lentiviral-Mediated Ex-Vivo Gene Therapy for Pediatric Patients with Severe Leukocyte Adhesion Deficiency-I (LAD-I): Interim Results
저자
by
Elena Almarza
;
Brian C. Beard
;
Theodore B. Moore
;
Gayatri R Rao
;
Claire Booth
, et al.
소스
Blood
. 138:2932-2932
Full Text (ScienceDirect O/A)
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7 .
The downregulated membrane expression of CD18 in CD34+ cells defines a primitive population of human hematopoietic stem cells
저자
by
Juan A. Bueren
;
Carlos Damián
;
Elena Almarza
;
Cristina Mesa-Núñez
;
Rebeca Sanchez
, et al.
소스
Stem Cell Research & Therapy
Stem Cell Research & Therapy, Vol 11, Iss 1, Pp 1-9 (2020)
Open Access (BioMed Central)
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7 .
A Phase 1/2 Study of Lentiviral-Mediated Ex-Vivo Gene Therapy for Pediatric Patients with Severe Leukocyte Adhesion Deficiency-I (LAD-I): Results from Phase 1
저자
by
Elena Almarza
;
Dayna Terrazas
;
Donald B. Kohn
;
Juan A. Bueren
;
Julián Sevilla
, et al.
소스
Blood
. 136:15-15
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7 .
A New Molecular Variant in the PTGS1 Gene That Abrogates Generation of Thromboxane A2 Synthesis and Associates with Platelet Dysfunction and Bleeding
저자
by
Jose Maria Bastida
;
José Rivera
;
Jesús María Hernández-Rivas
;
Maria Luisa Lozano
;
Matthew L. Edin
, et al.
소스
Blood
. 134:2375-2375
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