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1 . Academic Journal
Adeno-associated virus-mediated gene therapy in a patient with Canavan disease using dual routes of administration and immune modulation
저자
by
Manuela Corti
;
Barry J. Byrne
;
Dominic J. Gessler
;
Grace Thompson
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Samantha Norman
, et al.
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Molecular Therapy: Methods & Clinical Development, Vol 30, Iss , Pp 303-314 (2023)
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7 . Academic Journal
Diaphragm pacing and independent breathing in individuals with severe Pompe disease
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by
Cristina Liberati
;
Barry J. Byrne
;
David D. Fuller
;
Chasen Croft
;
Teresa Pitts
, et al.
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Frontiers in Rehabilitation Sciences, Vol 4 (2023)
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7 .
Preclinical Gene Therapy Studies for Metabolic Myopathy
저자
by
Barry J. Byrne
;
Manuela Corti
;
Cristina Liberati
;
Stephanie Salabarria
.
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Muscle Gene Therapy ISBN: 9783030030940
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6 .
Clinical Gene Therapy Trials for Pompe Disease
저자
by
Barry J. Byrne
;
Stephanie Salabarria
;
Manuela Corti
;
Cristina Liberati
.
소스
Muscle Gene Therapy ISBN: 9783030030940
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6 .
Popular Foods and Biodiversity Loss
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by
Cristina Liberati
;
Mildred L. Alvarado
;
Carly Kadlec
;
Tobias Lunt
;
Jessica Jones-Hughes
, et al.
소스
Promoting Biodiversity in Food Systems ISBN: 9781315212647
Promoting Biodiversity in Food Systems
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7 .
Safety of Intradiaphragmatic Delivery of Adeno-Associated Virus-Mediated Alpha-Glucosidase (rAAV1-CMV-hGAA) Gene Therapy in Children Affected by Pompe Disease
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by
Saleem Islam
;
Cristina Liberati
;
Roland W. Herzog
;
Shelley Collins
;
Lee Ann Lawson
, et al.
소스
Human gene therapy. Clinical development
. 28(4)
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7 .
Dietary factors in the risk of bladder cancer
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by
Cristina Liberati
;
Carlo La Vecchia
;
Barbara D'Avanzo
;
Silvia Franceschi
;
Adriano Decarli
, et al.
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Nutrition and cancer
. 12(1)
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