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1 . Academic Journal
Screening chimeric GAA variants in preclinicalstudy results in hematopoietic stem cell genetherapy candidate vectors for Pompe disease
저자
by
Yildirim Dogan
;
Cecilia N. Barese
;
Jeffrey W. Schindler
;
John K. Yoon
;
Zeenath Unnisa
, et al.
소스
Molecular Therapy: Methods & Clinical Development, Vol 27, Iss , Pp 464-487 (2022)
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7 . Academic Journal
Serum-free lentiviral vector production is compatible with medium-resident nuclease activity arising from adherent HEK293T host cells engineered with a nuclease-encoding transgene
저자
by
Sadfer Ali
;
Milena Rivera
;
John Ward
;
Eli Keshavarz-Moore
;
Chris Mason
, et al.
소스
Heliyon, Vol 9, Iss 6, Pp e17067- (2023)
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7 . Academic Journal
DNA methylation landscapes of 1538 breast cancers reveal a replication-linked clock, epigenomic instability and cis-regulation
저자
by
Rajbir Nath Batra
;
Aviezer Lifshitz
;
Ana Tufegdzic Vidakovic
;
Suet-Feung Chin
;
Ankita Sati-Batra
, et al.
소스
Nature Communications, Vol 12, Iss 1, Pp 1-13 (2021)
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7 . Academic Journal
Correction of pathology in mice displaying Gaucher disease type 1 by a clinically-applicable lentiviral vector
저자
by
Maria Dahl
;
Emma M.K. Smith
;
Sarah Warsi
;
Michael Rothe
;
Maria J. Ferraz
, et al.
소스
Molecular Therapy: Methods & Clinical Development, Vol 20, Iss , Pp 312-323 (2021)
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7 . Academic Journal
Gene Therapy Developments for Pompe Disease
저자
by
Zeenath Unnisa
;
John K. Yoon
;
Jeffrey W. Schindler
;
Chris Mason
;
Niek P. van Til
.
소스
Biomedicines, Vol 10, Iss 2, p 302 (2022)
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7 . Academic Journal
Directed differentiation of embryonic stem cells using a bead-based combinatorial screening method.
저자
by
Marina Tarunina
;
Diana Hernandez
;
Christopher J Johnson
;
Stanislav Rybtsov
;
Vidya Ramathas
, et al.
소스
PLoS ONE, Vol 9, Iss 9, p e104301 (2014)
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7 . Academic Journal
Microbial analysis of bite marks by sequence comparison of streptococcal DNA.
저자
by
Darnell M Kennedy
;
Jo-Ann L Stanton
;
José A García
;
Chris Mason
;
Christy J Rand
, et al.
소스
PLoS ONE, Vol 7, Iss 12, p e51757 (2012)
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7 . Academic Journal
Activation of pluripotency genes in human fibroblast cells by a novel mRNA based approach.
저자
by
Jordan R Plews
;
JianLiang Li
;
Mark Jones
;
Harry D Moore
;
Chris Mason
, et al.
소스
PLoS ONE, Vol 5, Iss 12, p e14397 (2010)
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7 .
High-throughput analysis of hematopoietic stem cell engraftment after intravenous and intracerebroventricular dosing
저자
by
Robert N. Plasschaert
;
Mark P. DeAndrade
;
Fritz Hull
;
Quoc Nguyen
;
Tara Peterson
, et al.
소스
Molecular Therapy
. 30:3209-3225
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7 .
The Effect of an Accelerated Renal Replacement Therapy Initiation Is Not Modified by Baseline Risk
저자
by
Federico Angriman
;
Bruno L. Ferreyro
;
Natalia Angeloni
;
Bruno R. da Costa
;
Ron Wald
, et al.
소스
ANNALS OF THE AMERICAN THORACIC SOCIETY
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