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1 . Academic Journal
Lentiviral gene therapy corrects platelet phenotype and function in patients with Wiskott-Aldrich syndrome
저자
by
Sereni, Lucia
;
Castiello, Maria Carmina
;
Di Silvestre, Dario
;
Della Valle, Patrizia
;
Brombin, Chiara
, et al.
소스
In
The Journal of Allergy and Clinical Immunology
September 2019 144(3):825-838
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7 . Academic Journal
B-cell reconstitution after lentiviral vector–mediated gene therapy in patients with Wiskott-Aldrich syndrome
저자
by
Castiello, Maria Carmina
;
Scaramuzza, Samantha
;
Pala, Francesca
;
Ferrua, Francesca
;
Uva, Paolo
, et al.
소스
In
The Journal of Allergy and Clinical Immunology
September 2015 136(3):692-702
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7 . Academic Journal
Exonic knockout and knockin gene editing in hematopoietic stem and progenitor cells rescues RAG1 immunodeficiency.
저자
by
Castiello, Maria Carmina
;
Brandas, Chiara
;
Ferrari, Samuele
;
Porcellini, Simona
;
Sacchetti, Nicolò
, et al.
소스
Science Translational Medicine; 2/7/2024, Vol. 16 Issue 733, p1-18, 18p
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7 . Academic Journal
B-cell development and functions and therapeutic options in adenosine deaminase–deficient patients
저자
by
Brigida, Immacolata
;
Sauer, Aisha V.
;
Ferrua, Francesca
;
Giannelli, Stefania
;
Scaramuzza, Samantha
, et al.
소스
In
The Journal of Allergy and Clinical Immunology
March 2014 133(3):799-806
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7 . Academic Journal
Partial correction of immunodeficiency by lentiviral vector gene therapy in mouse models carrying Rag1 hypomorphic mutations.
저자
by
Castiello, Maria Carmina
;
Di Verniere, Martina
;
Draghici, Elena
;
Fontana, Elena
;
Penna, Sara
, et al.
소스
Frontiers in Immunology; 2023, p1-19, 19p
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7 . Academic Journal
Revertant T lymphocytes in a patient with Wiskott-Aldrich syndrome: Analysis of function and distribution in lymphoid organs
저자
by
Trifari, Sara
;
Scaramuzza, Samantha
;
Catucci, Marco
;
Ponzoni, Maurilio
;
Mollica, Luca
, et al.
소스
In
The Journal of Allergy and Clinical Immunology
2010 125(2):439-448
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7 . Academic Journal
Towards Clinical Translation of Hematopoietic Cell Gene Editing for Treating Hyper-IgM Type 1
저자
by
Vavassori, Valentina
;
Mercuri, Elisabetta
;
Marcovecchio, Genni
;
Castiello, Maria Carmina
;
Canarutto, Daniele
, et al.
소스
In
Blood
23 November 2021 138 Supplement 1:3978-3978
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7 . Academic Journal
Thymic Epithelial Cell Alterations and Defective Thymopoiesis Lead to Central and Peripheral Tolerance Perturbation in MHCII Deficiency.
저자
by
Ferrua, Francesca
;
Bortolomai, Ileana
;
Fontana, Elena
;
Di Silvestre, Dario
;
Rigoni, Rosita
, et al.
소스
Frontiers in Immunology; 6/15/2021, Vol. 12, p1-20, 20p
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7 . Academic Journal
Innovative Cell-Based Therapies and Conditioning to Cure RAG Deficiency.
저자
by
Villa, Anna
;
Capo, Valentina
;
Castiello, Maria Carmina
.
소스
Frontiers in Immunology; 11/19/2020, Vol. 11, pN.PAG-N.PAG, 10p
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5 . Academic Journal
Autonomous role of Wiskott-Aldrich syndrome platelet deficiency in inducing autoimmunity and inflammation.
저자
by
Sereni, Lucia
;
Castiello, Maria Carmina
;
Marangoni, Francesco
;
Anselmo, Achille
;
di Silvestre, Dario
, et al.
소스
Journal of Allergy & Clinical Immunology; Oct2018, Vol. 142 Issue 4, p1272-1284, 13p
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