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1 . Academic Journal
In vivo lentiviral vector gene therapy to cure hereditary tyrosinemia type 1 and prevent development of precancerous and cancerous lesions
저자
by
Clara T. Nicolas
;
Caitlin J. VanLith
;
Raymond D. Hickey
;
Zeji Du
;
Lori G. Hillin
, et al.
소스
Nature Communications, Vol 13, Iss 1, Pp 1-15 (2022)
Open Access (DOAJ)
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7 . Academic Journal
Ex Vivo Cell Therapy by Ectopic Hepatocyte Transplantation Treats the Porcine Tyrosinemia Model of Acute Liver Failure
저자
by
Clara T. Nicolas
;
Robert A. Kaiser
;
Raymond D. Hickey
;
Kari L. Allen
;
Zeji Du
, et al.
소스
Molecular Therapy: Methods & Clinical Development, Vol 18, Iss , Pp 738-750 (2020)
Full Text (ScienceDirect)
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7 .
Use of an adeno‐associated virus serotype Anc80 to provide durable cure of phenylketonuria in a mouse model
저자
by
Michael Martinez
;
Nicholas D. Weber
;
William Cao
;
Lori G Hillin
;
Robert A. Kaiser
, et al.
소스
Journal of Inherited Metabolic Disease
. 44:1369-1381
Open Access (OpenAIRE)
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7 .
Ex Vivo Cell Therapy by Ectopic Hepatocyte Transplantation Treats the Porcine Tyrosinemia Model of Acute Liver Failure
저자
by
Bruce Amiot
;
Timothy R. DeGrado
;
Amin Cheikhi
;
Caitlin J. VanLith
;
Val J. Lowe
, et al.
소스
Molecular Therapy: Methods & Clinical Development, Vol 18, Iss, Pp 738-750 (2020)
Molecular Therapy. Methods & Clinical Development
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7 .
The Combination of Venetoclax and Ixazomib Selectively and Efficiently Kills HIV-Infected Cell Lines but Has Unacceptable Toxicity in Primary Cell Models
저자
by
Andrew D. Badley
;
Caitlin J. VanLith
;
Anisha Misra
;
Sekar Natesampillai
;
Ashton Krogman
, et al.
소스
J Virol
Full Text (ASM)
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Scopus
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7 .
In vivo lentiviral vector gene therapy to cure hereditary tyrosinemia type 1 and prevent development of precancerous and cancerous lesions
저자
by
Clara T. Nicolas
;
Caitlin J. VanLith
;
Raymond D. Hickey
;
Zeji Du
;
Lori G. Hillin
, et al.
소스
Nature communications
. 13(1)
Open Access (OpenAIRE)
Scopus
JCR 저널정보
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7 .
In vivo lentiviral vector gene therapy to cure hereditary tyrosinemia type 1 and prevent development of precancerous and cancerous lesions
저자
by
Joseph B. Lillegard
;
Aditya Bhagwate
;
Lori G Hillin
;
Daniel R. O'Brien
;
Kari L. Allen
, et al.
소스
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요약보기
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7 .
Ex Vivo Hepatocyte Reprograming Promotes Homology‐Directed DNA Repair to Correct Metabolic Disease in Mice After Transplantation
저자
by
Kari L. Allen
;
Jennifer Anne Chilton
;
Clara T. Nicolas
;
Rebekah M. Guthman
;
Robert A. Kaiser
, et al.
소스
Hepatology Communications
Open Access (OpenAIRE)
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7 .
Autologous Gene and Cell Therapy Provides Safe and Long-Term Curative Therapy in A Large Pig Model of Hereditary Tyrosinemia Type 1
저자
by
Caitlin J. VanLith
;
Harvey S. Chen
;
Kari L. Allen
;
Faysal Elgilani
;
Scott L. Nyberg
, et al.
소스
Cell Transplantation
Cell Transplantation, Vol 28 (2019)
Full Text (Sage OA)
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7 .
Curative Ex Vivo Hepatocyte-Directed Gene Editing in a Mouse Model of Hereditary Tyrosinemia Type 1
저자
by
Kari L. Allen
;
Clara T. Nicolas
;
Rebekah M. Guthman
;
Zeji Du
;
Joseph B. Lillegard
, et al.
소스
Human Gene Therapy
. 29:1315-1326
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