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1 . Academic Journal
Lentiviral correction of enzymatic activity restrains macrophage inflammation in adenosine deaminase 2 deficiency
저자
by
Zoccolillo, Matteo
;
Brigida, Immacolata
;
Barzaghi, Federica
;
Scala, Serena
;
Hernández, Raisa Jofra
, et al.
소스
In
Blood Advances
24 August 2021 5(16):3174-3187
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7 . Academic Journal
Lentiviral haemopoietic stem/progenitor cell gene therapy for treatment of Wiskott-Aldrich syndrome: interim results of a non-randomised, open-label, phase 1/2 clinical study
저자
by
Ferrua, Francesca
;
Cicalese, Maria Pia
;
Galimberti, Stefania
;
Giannelli, Stefania
;
Dionisio, Francesca
, et al.
소스
In
The Lancet Haematology
May 2019 6(5):e239-e253
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7 . Academic Journal
T-cell defects in patients with ARPC1B germline mutations account for combined immunodeficiency
저자
by
Brigida, Immacolata
;
Zoccolillo, Matteo
;
Cicalese, Maria Pia
;
Pfajfer, Laurène
;
Barzaghi, Federica
, et al.
소스
In
Blood
29 November 2018 132(22):2362-2374
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7 . Academic Journal
The case of an APDS patient: Defects in maturation and function and decreased in vitro anti-mycobacterial activity in the myeloid compartment
저자
by
Chiriaco, Maria
;
Brigida, Immacolata
;
Ariganello, Paola
;
Di Cesare, Silvia
;
Di Matteo, Gigliola
, et al.
소스
In
Clinical Immunology
May 2017 178:20-28
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7 . Academic Journal
Update on the safety and efficacy of retroviral gene therapy for immunodeficiency due to adenosine deaminase deficiency
저자
by
Cicalese, Maria Pia
;
Ferrua, Francesca
;
Castagnaro, Laura
;
Pajno, Roberta
;
Barzaghi, Federica
, et al.
소스
In
Blood
7 July 2016 128(1):45-54
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7 . Academic Journal
B-cell reconstitution after lentiviral vector–mediated gene therapy in patients with Wiskott-Aldrich syndrome
저자
by
Castiello, Maria Carmina
;
Scaramuzza, Samantha
;
Pala, Francesca
;
Ferrua, Francesca
;
Uva, Paolo
, et al.
소스
In
The Journal of Allergy and Clinical Immunology
September 2015 136(3):692-702
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7 . Academic Journal
B-cell development and functions and therapeutic options in adenosine deaminase–deficient patients
저자
by
Brigida, Immacolata
;
Sauer, Aisha V.
;
Ferrua, Francesca
;
Giannelli, Stefania
;
Scaramuzza, Samantha
, et al.
소스
In
The Journal of Allergy and Clinical Immunology
March 2014 133(3):799-806
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7 . Academic Journal
T-cell suicide gene therapy prompts thymic renewal in adults after hematopoietic stem cell transplantation
저자
by
Vago, Luca
;
Oliveira, Giacomo
;
Bondanza, Attilio
;
Noviello, Maddalena
;
Soldati, Corrado
, et al.
소스
In
Blood
30 August 2012 120(9):1820-1830
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7 . Academic Journal
HIV-1 envelope-dependent restriction of CXCR4-using viruses in child but not adult untransformed CD4+ T-lymphocyte lines
저자
by
Mariani, Samanta A.
;
Brigida, Immacolata
;
Kajaste-Rudnitski, Anna
;
Ghezzi, Silvia
;
Rocchi, Alessia
, et al.
소스
In
Blood
1 March 2012 119(9):2013-2023
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7 . Academic Journal
Alterations in the adenosine metabolism and CD39/CD73 adenosinergic machinery cause loss of Treg cell function and autoimmunity in ADA-deficient SCID
저자
by
Sauer, Aisha V.
;
Brigida, Immacolata
;
Carriglio, Nicola
;
Jofra Hernandez, Raisa
;
Scaramuzza, Samantha
, et al.
소스
In
Blood
9 February 2012 119(6):1428-1439
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