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1 . Academic Journal
Clinical and functional efficacy of elexacaftor/tezacaftor/ivacaftor in people with cystic fibrosis carrying the N1303K mutation
저자
by
Sadras, Ido
;
Kerem, Eitan
;
Livnat, Galit
;
Sarouk, Ifat
;
Breuer, Oded
, et al.
소스
In
Journal of Cystic Fibrosis
November 2023 22(6):1062-1069
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7 . Academic Journal
Riociguat for the treatment of Phe508del homozygous adults with cystic fibrosis
저자
by
Derichs, Nico
;
Taylor-Cousar, Jennifer L.
;
Davies, Jane C.
;
Fajac, Isabelle
;
Tullis, Elizabeth
, et al.
소스
In
Journal of Cystic Fibrosis
November 2021 20(6):1018-1025
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7 . Academic Journal
Identification of binding sites for ivacaftor on the cystic fibrosis transmembrane conductance regulator
저자
by
Laselva, Onofrio
;
Qureshi, Zafar
;
Zeng, Zhi-Wei
;
Petrotchenko, Evgeniy V.
;
Ramjeesingh, Mohabir
, et al.
소스
In
iScience
25 June 2021 24(6)
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7 . Academic Journal
Emerging preclinical modulators developed for F508del-CFTR have the potential to be effective for ORKAMBI resistant processing mutants
저자
by
Laselva, Onofrio
;
Bartlett, Claire
;
Popa, Alec
;
Ouyang, Hong
;
Gunawardena, Tarini N.A.
, et al.
소스
In
Journal of Cystic Fibrosis
January 2021 20(1):106-119
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7 . Academic Journal
The CF Canada-Sick Kids Program in individual CF therapy: A resource for the advancement of personalized medicine in CF
저자
by
Eckford, Paul D.W.
;
McCormack, Jacqueline
;
Munsie, Lise
;
He, Gengming
;
Stanojevic, Sanja
, et al.
소스
In
Journal of Cystic Fibrosis
January 2019 18(1):35-43
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7 . Academic Journal
Synthesis and characterization of a photoaffinity labelling probe based on the structure of the cystic fibrosis drug ivacaftor
저자
by
Hamilton, C. Michael
;
Hung, Maurita
;
Chen, Gang
;
Qureshi, Zafar
;
Thompson, John R.
, et al.
소스
In
Tetrahedron
20 September 2018 74(38):5528-5538
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7 . Academic Journal
Facilitating Structure-Function Studies of CFTR Modulator Sites with Efficiencies in Mutagenesis and Functional Screening
저자
by
Molinski, Steven V.
;
Ahmadi, Saumel
;
Hung, Maurita
;
Bear, Christine E.
.
소스
In
SLAS Discovery
December 2015 20(10):1204-1217
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6 . Academic Journal
VX-809 and Related Corrector Compounds Exhibit Secondary Activity Stabilizing Active F508del-CFTR after Its Partial Rescue to the Cell Surface
저자
by
Eckford, Paul D.W.
;
Ramjeesingh, Mohabir
;
Molinski, Steven
;
Pasyk, Stan
;
Dekkers, Johanna F.
, et al.
소스
In
Chemistry & Biology
22 May 2014 21(5):666-678
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7 . Academic Journal
A Cell-Based Optimised Approach for Rapid and Efficient Gene Editing of Human Pluripotent Stem Cells.
저자
by
Cuevas-Ocaña, Sara
;
Yang, Jin Ye
;
Aushev, Magomet
;
Schlossmacher, George
;
Bear, Christine E.
, et al.
소스
International Journal of Molecular Sciences
. Jun2023, Vol. 24 Issue 12, p10266. 24p.
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7 . Academic Journal
Validating organoid-derived human intestinal monolayers for personalized therapy in cystic fibrosis.
저자
by
Birimberg-Schwartz, Liron
;
Ip, Wan
;
Bartlett, Claire
;
Avolio, Julie
;
Vonk, Annelotte M.
, et al.
소스
Life Science Alliance; Jun2023, Vol. 6 Issue 6, p1-13, 13p
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