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1 . Academic Journal
Characterization of pulmonary function in 10–18 year old patients with Duchenne muscular dystrophy
저자
by
Bernert, G.
;
Knipp, F.
;
Buyse, G.M.
;
Goemans, N.
;
Van den Hauwe, M.
, et al.
소스
In
Neuromuscular Disorders
April 2017 27(4):307-314
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7 . Academic Journal
Idebenone reduces respiratory complications in patients with Duchenne muscular dystrophy
저자
by
Bernert, G.
;
Knipp, F.
;
Buyse, G.M.
;
Goemans, N.
;
van den Hauwe, M.
, et al.
소스
In
Neuromuscular Disorders
August 2016 26(8):473-480
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7 . Academic Journal
P85 External responsiveness of the Duchenne video assessment, a novel fit-for-purpose remotely collected outcome measure for Duchenne muscular dystrophy
저자
by
Wilson, S.
;
Contesse, M.
;
Brown, C.
;
Gensler, G.
;
Karri, V.
, et al.
소스
In
Neuromuscular Disorders
October 2023 33 Supplement 1:S166-S166
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7 . Academic Journal
P77 A 12-tier functional scale for spinal muscular atrophy
저자
by
Burk, M Moore
;
Crawford, T.
;
Krosschell, K.
;
Apkon, S.
.
소스
In
Neuromuscular Disorders
October 2023 33 Supplement 1:S136-S136
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6 . Academic Journal
P.220 Neuropsychological functioning in CMT type 2Z: A case report of language deficits masquerading as intellectual disability
저자
by
Miele, A.
;
Yang, M.
;
Apkon, S.
;
Silver, C.
;
Gibbons, M.
, et al.
소스
In
Neuromuscular Disorders
October 2022 32 Supplement 1:S135-S135
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7 . Academic Journal
G.P.44 - Addressing discrepancies in care with the certified Duchenne care center program
저자
by
Kinnett, K.
;
Mendel, J.
;
Dowling, J.
;
Wagner, E.
;
Cripe, L.
, et al.
소스
In
Neuromuscular Disorders
October 2015 25 Supplement 2:S199-S200
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7 .
Towards regulatory endorsement of drug development tools to promote the application of model-informed drug development in Duchenne muscular dystrophy
저자
by
Conrado, D. J.
;
Larkindale, J.
;
Berg, A.
;
Hill, M.
;
Burton, J.
, et al.
소스
Journal of pharmacokinetics and pharmacodynamics
. 46(5)
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7 .
Characterization of pulmonary function in 10–18 year old patients with Duchenne muscular dystrophy
저자
by
Ulrike Schara
;
Diana Castro
;
T. Gidaro
;
S. Lutz
;
Ksenija Gorni
, et al.
소스
Europe PubMed Central
Neuromuscular Disorders, 27(4), 307-314
Open Access (OpenAIRE)
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7 .
Treatment effect of idebenone on inspiratory function in patients with Duchenne muscular dystrophy
저자
by
Buyse, G.M.
;
Voit, Thomas
;
Schara, Ulrike
;
Straathof, C.S.M.
;
D’Angelo, M.G.
, et al.
소스
Pediatric Pulmonology
Neuromuscular Disorders, 26, S156-S157
r-IIS La Fe. Repositorio Institucional de Producción Científica del Instituto de Investigación Sanitaria La Fe
instname
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7 . Academic Journal
SMA THERAPIES I: P.171Transforaminal intrathecal delivery of nusinersen using cone-beam computed tomography in children with spinal muscular atrophy: results of technical success and safety.
저자
by
Apkon, S.
;
Weaver, J.
;
Natarajan, N.
;
Shaw, D.
;
Koo, K.
, et al.
소스
Neuromuscular Disorders
. Oct2018:Supplement 2, Vol. 28, pS80-S80. 1p.
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