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1 . Academic Journal
S270: TRANSFUSION INDEPENDENCE AFTER EXAGAMGLOGENE AUTOTEMCEL IN PATIENTS WITH TRANSFUSION-DEPENDENT ΒETA-THALASSEMIA
저자
by
Franco Locatelli
;
Peter Lang
;
Selim Corbacioglu
;
Amanda LI
;
Josu De La Fuente
, et al.
소스
HemaSphere, Vol 7, p e8473180 (2023)
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7 .
The diagnosis of severe combined immunodeficiency (SCID): The Primary Immune Deficiency Treatment Consortium (PIDTC) 2022 Definitions
저자
by
Christopher C. Dvorak
;
Elie Haddad
;
Jennifer Heimall
;
Elizabeth Dunn
;
Rebecca H. Buckley
, et al.
소스
Journal of Allergy and Clinical Immunology
. 151:539-546
Full Text (Clinical Key)
Open Access (OpenAIRE)
Web of Science
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7 .
Viral‐specific T cells for Cytomegalovirus retinitis following hematopoietic stem cell transplantation: A success story
저자
by
Raul Montiel‐Esparza
;
Suzanne M. Michalak
;
Anthony Huy Dinh Le
;
Christopher Or
;
Quan Dong Nguyen
, et al.
소스
Pediatric Blood & Cancer
.
Full Text (Wiley)
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7 .
Efficacy and Safety of a Single Dose of Exagamglogene Autotemcel for Transfusion-Dependent β-Thalassemia
저자
by
Franco Locatelli
;
Peter Lang
;
Amanda Li
;
Selim Corbacioglu
;
Josu de la Fuente
, et al.
소스
Blood
. 140:4899-4901
Full Text (ScienceDirect O/A)
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7 .
Sequential Stem Cell–Kidney Transplantation in Schimke Immuno-osseous Dysplasia
저자
by
Alice Bertaina
;
Paul C. Grimm
;
Kenneth Weinberg
;
Robertson Parkman
;
Karen M. Kristovich
, et al.
소스
New England Journal of Medicine
. 386:2295-2302
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7 .
Diaphragmatic Thickening Fraction by Ultrasound in Mechanically Ventilated Pediatric Patients: Pilot Observations During Spontaneous Breathing Trials
저자
by
Ami J. Shah
;
Kitman Wai
;
Matthew P. Sharron
;
Marisa Mize
;
Joanna Cohen
, et al.
소스
Journal of Ultrasound in Medicine
. 41:3043-3050
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7 .
Data from Infusion of Alloanergized Donor Lymphocytes after CD34-selected Haploidentical Myeloablative Hematopoietic Stem Cell Transplantation
저자
by
Eva C. Guinan
;
Lee M. Nadler
;
Richard E. Champlin
;
Peter F. Thall
;
Laurence J. Cooper
, et al.
소스
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7 .
Supplementary Methods, Tables S1-4, Figures S1-4 from Infusion of Alloanergized Donor Lymphocytes after CD34-selected Haploidentical Myeloablative Hematopoietic Stem Cell Transplantation
저자
by
Eva C. Guinan
;
Lee M. Nadler
;
Richard E. Champlin
;
Peter F. Thall
;
Laurence J. Cooper
, et al.
소스
Open Access (OpenAIRE)
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7 .
The diagnosis of severe combined immunodeficiency: Implementation of the PIDTC 2022 Definitions
저자
by
Christopher C. Dvorak
;
Elie Haddad
;
Jennifer Heimall
;
Elizabeth Dunn
;
Morton J. Cowan
, et al.
소스
The Journal of allergy and clinical immunology
.
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7 .
Autologous Ex Vivo Lentiviral Gene Therapy for Adenosine Deaminase Deficiency
저자
by
Donald B. Kohn
;
Claire Booth
;
Kit L. Shaw
;
Jinhua Xu-Bayford
;
Elizabeth Garabedian
, et al.
소스
N Engl J Med
The New England journal of medicine, vol 384, iss 21
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