Bush, J A, Meyer, S M, Fuerst, R, Tong, Y, Li, Y, Benhamou, R I, Aikawa, H, Zanon, P R A, Gibaut, Q M R, Angelbello, A J, Gendron, T F, Zhang, Y J, Petrucelli, L, Heick Jensen, T, Childs-Disney, J L & Disney, M D 2022, ' A blood-brain penetrant RNA-targeted small molecule triggers elimination of r(G 4 C 2 ) exp in c9ALS/FTD via the nuclear RNA exosome ', Proceedings of the National Academy of Sciences of the United States of America, vol. 119, no. 48, e2210532119 . https://doi.org/10.1073/pnas.2210532119