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1 . Academic Journal
Novel AAV variants with improved tropism for human Schwann cells
저자
by
Drouyer, Matthieu
;
Chu, Tak-Ho
;
Labit, Elodie
;
Haase, Florencia
;
Navarro, Renina Gale
, et al.
소스
In
Molecular Therapy - Methods & Clinical Development
13 June 2024 32(2)
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7 . Academic Journal
AAV-delivered hepato-adrenal cooperativity in steroidogenesis: Implications for gene therapy for congenital adrenal hyperplasia
저자
by
Graves, Lara E.
;
van Dijk, Eva B.
;
Zhu, Erhua
;
Koyyalamudi, Sundar
;
Wotton, Tiffany
, et al.
소스
In
Molecular Therapy - Methods & Clinical Development
13 June 2024 32(2)
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7 . Academic Journal
Development of CNS tropic AAV1-like variants with reduced liver-targeting following systemic administration in mice
저자
by
Drouyer, Matthieu
;
Merjane, Jessica
;
Nazareth, Deborah
;
Knight, Maddison
;
Scott, Suzanne
, et al.
소스
In
Molecular Therapy
6 March 2024 32(3):818-836
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7 . Academic Journal
Development of new adeno-associated virus capsid variants for targeted gene delivery to human cardiomyocytes
저자
by
Kok, Cindy Y.
;
Tsurusaki, Shinya
;
Cabanes-Creus, Marti
;
Igoor, Sindhu
;
Rao, Renuka
, et al.
소스
In
Molecular Therapy - Methods & Clinical Development
14 September 2023 30:459-473
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7 . Academic Journal
Structural and functional characterization of capsid binding by anti-AAV9 monoclonal antibodies from infants after SMA gene therapy
저자
by
Logan, Grant J.
;
Mietzsch, Mario
;
Khandekar, Neeta
;
D’Silva, Arlene
;
Anderson, Daniel
, et al.
소스
In
Molecular Therapy
5 July 2023 31(7):1979-1993
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7 . Academic Journal
Gene Therapy for Paediatric Homozygous Familial Hypercholesterolaemia
저자
by
Graves, Lara E.
;
Horton, Ari
;
Alexander, Ian E.
;
Srinivasan, Shubha
.
소스
In
Heart, Lung and Circulation
July 2023 32(7):769-779
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6 . Academic Journal
In Search of Adeno-Associated Virus Vectors With Enhanced Cardiac Tropism for Gene Therapy
저자
by
Sasaki, Natsuki
;
Kok, Cindy Y.
;
Westhaus, Adrian
;
Alexander, Ian E.
;
Lisowski, Leszek
, et al.
소스
In
Heart, Lung and Circulation
July 2023 32(7):816-824
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7 . Academic Journal
Characterization of the humanized FRG mouse model and development of an AAV-LK03 variant with improved liver lobular biodistribution
저자
by
Cabanes-Creus, Marti
;
Navarro, Renina Gale
;
Liao, Sophia H.Y.
;
Scott, Suzanne
;
Carlessi, Rodrigo
, et al.
소스
In
Molecular Therapy - Methods & Clinical Development
9 March 2023 28:220-237
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7 . Academic Journal
Efficient in vivo editing of OTC-deficient patient-derived primary human hepatocytes
저자
by
Ginn, Samantha L.
;
Amaya, Anais K.
;
Liao, Sophia H.Y.
;
Zhu, Erhua
;
Cunningham, Sharon C.
, et al.
소스
In
JHEP Reports
February 2020 2(1)
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7 . Academic Journal
Human Connexin40 Mutations Slow Conduction and Increase Propensity for Atrial Fibrillation
저자
by
Kanthan, Ajita
;
Fahmy, Peter
;
Rao, Renuka
;
Pouliopoulos, Jim
;
Alexander, Ian E.
, et al.
소스
In
Heart, Lung and Circulation
January 2018 27(1):114-121
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