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1 . Academic Journal
The value of knowing: preferences for genetic testing to diagnose rare muscle diseases
저자
by
Carol Mansfield
;
Marco Boeri
;
Josh Coulter
;
Eileen Baranowski
;
Susan Sparks
, et al.
소스
Orphanet Journal of Rare Diseases, Vol 19, Iss 1, Pp 1-11 (2024)
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7 . Academic Journal
Applying the win ratio method in clinical trials of orphan drugs: an analysis of data from the COMET trial of avalglucosidase alfa in patients with late-onset Pompe disease
저자
by
Matthias Boentert
;
Kenneth I. Berger
;
Jordi Díaz-Manera
;
Mazen M. Dimachkie
;
Alaa Hamed
, et al.
소스
Orphanet Journal of Rare Diseases, Vol 19, Iss 1, Pp 1-8 (2024)
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7 . Academic Journal
Caffeine-folic acid-loaded-chitosan nanoparticles combined with methotrexate as a novel HepG2 immunotherapy targeting adenosine A2A receptor downstream cascade
저자
by
Alaa Hamed
;
Doaa Ghareeb
;
Tarek M. Mohamed
;
Mahmoud Hamed
;
Mohammed S. Nofal
, et al.
소스
BMC Complementary Medicine and Therapies, Vol 23, Iss 1, Pp 1-24 (2023)
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7 . Academic Journal
Variation of caesarean section rates in Palestinian governmental hospitals
저자
by
Aisha Shalash
;
Yasmeen Wahdan
;
Hasan M. M. Alsalman
;
Ala’a Jamal Kamel Shehab
;
Tayseer Afifi
, et al.
소스
BMC Pregnancy and Childbirth, Vol 22, Iss 1, Pp 1-10 (2022)
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7 . Academic Journal
Qualitative interviews to improve patient-reported outcome measures in late-onset Pompe disease: the patient perspective
저자
by
Alaa Hamed
;
Kristina An Haack
;
Chad Gwaltney
;
Eileen Baranowski
;
Andrew Stewart
, et al.
소스
Orphanet Journal of Rare Diseases, Vol 16, Iss 1, Pp 1-12 (2021)
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7 . Academic Journal
Development of the Fabry Disease Patient-Reported Outcome (FD-PRO): a new instrument to measure the symptoms and impacts of Fabry Disease
저자
by
Alaa Hamed
;
Pronabesh DasMahapatra
;
Nicole Lyn
;
Chad Gwaltney
;
Robert J. Hopkin
.
소스
Orphanet Journal of Rare Diseases, Vol 16, Iss 1, Pp 1-12 (2021)
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7 . Academic Journal
National mapping of schistosomiasis, soil-transmitted helminthiasis and anaemia in Yemen: Towards better national control and elimination.
저자
by
Nur Alia Johari
;
Dhekra Amin Annuzaili
;
Hani Farouk El-Talabawy
;
Maryam Ba-Break
;
Abdulsalam M Al-Mekhlafi
, et al.
소스
PLoS Neglected Tropical Diseases, Vol 16, Iss 3, p e0010092 (2022)
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7 . Academic Journal
Ondansetron Compared with Doxylamine and Pyridoxine for Treatment of Nausea and Vomiting in Pregnancy
저자
by
Mohamed Yahia
;
Khattab Khattab
;
Alaa Hamed
.
소스
International Journal of Medical Arts, Vol 2, Iss 3, Pp 611-618 (2020)
Open Access (DOAJ)
Find it @ DONGA
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5 . Academic Journal
Fabry Disease Patient-Reported Outcome (FD-PRO) demonstrates robust measurement properties for assessing symptom severity in Fabry disease
저자
by
Alaa Hamed
;
Pronabesh DasMahapatra
;
Nicole Lyn
;
Chad Gwaltney
;
Charlie Iaconangelo
, et al.
소스
Molecular Genetics and Metabolism Reports, Vol 29, Iss , Pp 100824- (2021)
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7 . Academic Journal
Patient and caregiver perspectives on burden of disease manifestations in late-onset Tay-Sachs and Sandhoff diseases
저자
by
Nicole Lyn
;
Ruth Pulikottil-Jacob
;
Camille Rochmann
;
Robert Krupnick
;
Chad Gwaltney
, et al.
소스
Orphanet Journal of Rare Diseases, Vol 15, Iss 1, Pp 1-14 (2020)
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