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1 . Academic Journal
Congenital dyserythropoietic anemia type I: First report from the Congenital Dyserythropoietic Anemia Registry of North America (CDAR)
저자
by
Husami, Ammar
;
Kalfa, Theodosia
;
Lorsbach, Robert
;
Lutzko, Carolyn
;
Nelson, Adam
, et al.
소스
In
Blood Cells, Molecules and Diseases
March 2021 87
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7 . Academic Journal
Eptacog Beta (rFVIIa) Has a Low Incidence of Spontaneous Rebleeding through 24 and 48 Hours in Adult and Adolescent Patients with Hemophilia A or B with Inhibitors
저자
by
Dunn, Amy L.
;
Dargaud, Yesim
;
Abajas, Yasmina L.
;
Carcao, Manuel
;
Castaman, Giancarlo
, et al.
소스
In
Blood
15 November 2022 140 Supplement 1:8485-8488
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7 . Academic Journal
Congenital Dyserythropoietic Anemia Type II: An Update from the Congenital Dyseryhtropoietic Anemia Registry of North America (CDAR)
저자
by
Elgammal, Yasmin
;
Risinger, Mary
;
Husami, Ammar
;
Walden, Joseph
;
Gupta, Sweta
, et al.
소스
In
Blood
2 November 2023 142 Supplement 1:1079-1079
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7 . Academic Journal
Use of plasma‐derived factor X concentrate in neonates and infants with congenital factor X deficiency
저자
by
Zimowski, Karen L.
;
McGuinn, Catherine E.
;
Abajas, Yasmina L.
;
Schultz, Corinna L.
;
Kaicker, Shipra
, et al.
소스
In
Journal of Thrombosis and Haemostasis
October 2020 18(10):2551-2556
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7 . Academic Journal
Quality of life in a large multinational haemophilia B cohort (The B‐Natural study) – Unmet needs remain.
저자
by
Berntorp, Erik
;
LeBeau, Petra
;
Ragni, Margaret V.
;
Borhany, Munira
;
Abajas, Yasmina L.
, et al.
소스
Haemophilia
. May2022, Vol. 28 Issue 3, p453-461. 9p. 1 Chart, 2 Graphs.
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7 . Academic Journal
The B‐Natural study—The outcome of immune tolerance induction therapy in patients with severe haemophilia B.
저자
by
Astermark, Jan
;
Holstein, Katharina
;
Abajas, Yasmina L.
;
Kearney, Susan
;
Croteau, Stacy E.
, et al.
소스
Haemophilia
. Sep2021, Vol. 27 Issue 5, p802-813. 12p. 1 Diagram, 2 Charts, 2 Graphs.
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7 . Academic Journal
Natural history study of factor IX deficiency with focus on treatment and complications (B‐Natural).
저자
by
Shapiro, Amy D.
;
Ragni, Margaret V.
;
Borhany, Munira
;
Abajas, Yasmina L.
;
Tarantino, Michael D.
, et al.
소스
Haemophilia
. Jan2021, Vol. 27 Issue 1, p49-59. 11p. 1 Diagram, 5 Charts, 2 Graphs.
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7 . Periodical
Superior human hepatocyte transduction with adeno-associated virus vector serotype 7
저자
by
Shao, Wenwei
;
Pei, Xiaolei
;
Cui, Caibin
;
Askew, Charles
;
Dobbins, Amanda
, et al.
소스
Gene Therapy; December 2019, Vol. 26 Issue: 12 p504-514, 11p
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7 . Academic Journal
A Retrospective Study of the Cytokine Pro?le Changes in Mice with FVIII Inhibitor Development After Adeno-Associated Virus--Mediated Gene Therapy in a Hemophilia A Mouse Model.
저자
by
Junjiang Sun
;
Zhenhua Yuan
;
Abajas, Yasmina L.
;
Szollosi, Doreen E.
;
Genlin Hu
, et al.
소스
Human Gene Therapy
. Mar2018, Vol. 29 Issue 3, p381-389. 9p.
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7 . Book
Gene Therapy for Bleeding Disorders.
저자
by
Monahan, Paul E.
;
Abajas, Yasmina L.
.
소스
Nonmalignant Hematology; 2016, p321-336, 16p
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