Natural history, outcome, and treatment efficacy in children and adults with glutaryl-CoA dehydrogenase deficiency
- Resource Type
- Journal
- Authors
- Kolker, S; Garbade, SF; Greenberg, CR; Leonard, JV; Saudubray, JM; Ribes, A; Kalkanoglu, S; Lund, AM; Merinero, B; Wajner, M; Troncoso, M; Williams, M; Walter, JH; Campistol, J; Marti-Herrero, M; Caswill, M; Burlina, AB; Lagler, F; Maier, EM; Schwahn, B; Tokatli, A; Dursun, A; Coskun, T; Chalmers, RA; Koeller, DM; Zschocke, J; Christensen, E; Burgard, P; Hoffmann, GF
- Source
- PEDIATRIC RESEARCH; JUN 2006, 59 6, p840-p847, 8p.
- Subject
- Language
- English
- ISSN
- 00313998