Preclinical Evaluation of a Novel Lentiviral Vector Driving Lineage-Specific BCL11A Knockdown for Sickle Cell Gene Therapy
- Resource Type
- Journal
- Authors
- Brendel, Christian; Negre, Olivier; Rothe, Michael; Guda, Swaroopa; Parsons, Geoff; Harris, Chad; McGuinness, Meaghan; Abriss, Daniela; Tsytsykova, Alla; Klatt, Denise; Bentler, Martin; Pellin, Danilo; Christiansen, Lauryn; Schambach, Axel; Manis, John; Trebeden-Negre, Helene; Bonner, Melissa; Esrick, Erica; Veres, Gabor; Armant, Myriam; Williams, David A.
- Source
- MOLECULAR THERAPY-METHODS & CLINICAL DEVELOPMENT; JUN 12 2020, 17 p589-p600, 12p.
- Subject
- Language
- English
- ISSN
- 23290501