Preclinical Efficacy and Safety Evaluation of Hematopoietic Stem Cell Gene Therapy in a Mouse Model of MNGIE
- Resource Type
- Journal
- Authors
- Yadak, Rana; Cabrera-Perez, Raquel; Torres-Torronteras, Javier; Bugiani, Marianna; Haeck, Joost C.; Huston, Marshall W.; Bogaerts, Elly; Goffart, Steffi; Jacobs, Edwin H.; Stok, Merel; Leonardelli, Lorena; Biasco, Luca; Verdijk, Robert M.; Bernsen, Monique R.; Ruijter, George; Marti, Ramon; Wagemaker, Gerard; van Til, Niek P.; de Coo, Irenaeus F. M.
- Source
- MOLECULAR THERAPY-METHODS & CLINICAL DEVELOPMENT; MAR 2018, 8 p152-p165, 14p.
- Subject
- Language
- English
- ISSN
- 23290501