In vivo base editing of a pathogenic Eif2b5 variant improves vanishing white matter phenotypes in mice
- Resource Type
- Article
- Authors
- Böck, Desirée; Revers, Ilma M.; Bomhof, Anastasia S.J.; Hillen, Anne E.J.; Boeijink, Claire; Kissling, Lucas; Egli, Sabina; Moreno-Mateos, Miguel A.; van der Knaap, Marjo S.; van Til, Niek P.; Schwank, Gerald
- Source
- In Molecular Therapy 1 May 2024 32(5):1328-1343
- Subject
- Language
- ISSN
- 1525-0016