Evaluation of an AAV9-mini-dystrophin gene therapy candidate in a rat model of Duchenne muscular dystrophy
- Resource Type
- Article
- Authors
- Le Guiner, Caroline; Xiao, Xiao; Larcher, Thibaut; Lafoux, Aude; Huchet, Corinne; Toumaniantz, Gilles; Adjali, Oumeya; Anegon, Ignacio; Remy, Séverine; Grieger, Josh; Li, Juan; Farrokhi, Vahid; Neubert, Hendrik; Owens, Jane; McIntyre, Maritza; Moullier, Philippe; Samulski, R. Jude
- Source
- In Molecular Therapy - Methods & Clinical Development 14 September 2023 30:30-47
- Subject
- Language
- ISSN
- 2329-0501