LBP-008 AAV8 gene therapy for mitochondrial neurogastrointestinal encephalomyopathy
- Resource Type
- Abstract
- Authors
- Brevini, Teresa; Swift, Lisa; Reynolds, Helen; Stopforth, Richard; Malam, Yogeshkumar; Ong, John; Spiers, Harry; Jovanovic, Emilija; Scaravaglio, Miki; Vakeeswarasarma, Vitushan; Heslop, James; Hosgood, Sarah; Fuchs, Claudia; Trauner, Michael; Duckworth, Adam; Paterson, Anna; Kaser, Arthur; van Den Ameele, Jelle; Kosmoliaptsis, Vassillis; Webb, Gwilym; Watson, Christopher; Butler, Andrew; Sampaziotis, Fotios
- Source
- In Journal of Hepatology June 2024 80 Supplement 1:S81-S81
- Subject
- Language
- ISSN
- 0168-8278