Assessment of Systemic Delivery of rAAVrh74.MHCK7.micro-dystrophin in Children With Duchenne Muscular Dystrophy: A Nonrandomized Controlled Trial.
- Resource Type
- Article
- Authors
- Mendell, Jerry R.; Sahenk, Zarife; Lehman, Kelly; Nease, Carrie; Lowes, Linda P.; Miller, Natalie F.; Iammarino, Megan A.; Alfano, Lindsay N.; Nicholl, Amanda; Al-Zaidy, Samiah; Lewis, Sarah; Church, Kathleen; Shell, Richard; Cripe, Linda H.; Potter, Rachael A.; Griffin, Danielle A.; Pozsgai, Eric; Dugar, Ashish; Hogan, Mark; Rodino-Klapac, Louise R.
- Source
- JAMA Neurology; Sep2020, Vol. 77 Issue 9, p1122-1131, 10p
- Subject
- Language
- ISSN
- 21686149