Increase in Full-Length Dystrophin by Exon Skipping in Duchenne Muscular Dystrophy Patients with Single Exon Duplications: An Open-label Study.
- Resource Type
- Article
- Authors
- Nicolau, Stefan; Malhotra, Jyoti; Kaler, Maryann; Magistrado-Coxen, Pamela; Iammarino, Megan A.; Reash, Natalie F.; Frair, Emma C.; Wijeratne, Saranga; Kelly, Benjamin J.; White, Peter; Lowes, Linda P.; Waldrop, Megan A.; Flanigan, Kevin M.
- Source
- Journal of Neuromuscular Diseases; 2024, Vol. 11 Issue 3, p679-685, 7p
- Subject
- Language
- ISSN
- 22143599