Delivery of oligonucleotides to bone marrow to modulate ferrochelatase splicing in a mouse model of erythropoietic protoporphyria.
- Resource Type
- Article
- Source
- Nucleic Acids Research; 5/21/2020, Vol. 48 Issue 9, p4658-4671, 14p
- Subject
- Language
- ISSN
- 03051048