ZFN-mediated correction of murine MPS I model by expression of the human IDUA cDNA from the albumin “safe harbor” locus.
- Resource Type
- Article
- Authors
- Ou, Li; DeKelver, Russell; Tom, Susan; Radeke, Robert; Rhode, Michelle; Manning-Bog, Amy; Sproul, Scott; Przybilla, Michael J.; Koniar, Brenda L.; Podetz-Pedersen, Kelly M.; Laoharawee, Kanut; Cooksley, Renee D.; Holmes, Michael C.; Wechsler, Thomas; Scott McIvor, R.; Whitley, Chester B.
- Source
- Molecular Genetics & Metabolism. Feb2016, Vol. 117 Issue 2, pS89-S89. 1p.
- Subject
- *ZINC-finger proteins
*MUCOPOLYSACCHARIDOSIS I
*ANTISENSE DNA
*ALBUMINS
*MEDICATION safety
- Language
- ISSN
- 1096-7192