European Journal of Medical Genetics, 64(9):104281. Elsevier Masson Dhaenens, B A E, Ferner, R E, Evans, D G, Heimann, G, Potratz, C, van de Ketterij, E, Kaindl, A M, Hissink, G, Carton, C, Bakker, A, Nievo, M, Legius, E & Oostenbrink, R 2021, ' Lessons learned from drug trials in neurofibromatosis: A systematic review ', European journal of medical genetics, vol. 64, no. 9, 104281 . https://doi.org/10.1016/j.ejmg.2021.104281