Use of Defibrotide to help prevent post-transplant endothelial injury in a genetically predisposed infant with metachromatic leukodystrophy undergoing hematopoietic stem cell gene therapy
Resource Type
Letter
Authors
Calbi, Valeria ; Fumagalli, Francesca ; Consiglieri, Giulia ; Penati, Rachele ; Acquati, Serena ; Redaelli, Daniela ; Attanasio, Vanessa ; Marcella, Facchini ; Cicalese, Maria Pia ; Migliavacca, Maddalena ; Barzaghi, Federica ; Ferrua, Francesca ; Assanelli, Andrea ; Silvani, Paolo ; Zoccolillo, Matteo ; Chidini, Giovanna ; Chiesa, Robert ; Arora, Ruchi ; Ciotti, Francesca ; Sarzana, Marina ; Antonioli, Gigliola ; Baldoli, Cristina ; Morena, Francesco ; Martino, Sabata ; Ardissino, Gian Luigi ; Sora, Maria Grazia Natali ; Naldini, Luigi ; Ciceri, Fabio ; Aiuti, Alessandro ; Bernardo, Maria Ester
Source
Bone Marrow Transplantation: Official journal of the European Society for Blood and Marrow Transplantation . 53(7):913-917
Subject
Language
English
ISSN
0268-3369 1476-5365