Rycal S48168 (ARM210) for RYR1-related myopathies: a phase one, open-label, dose-escalation trial
- Resource Type
- Article
- Authors
- Todd, Joshua J.; Lawal, Tokunbor A.; Chrismer, Irene C.; Kokkinis, Angela; Grunseich, Christopher; Jain, Minal S.; Waite, Melissa R.; Biancavilla, Victoria; Pocock, Shavonne; Brooks, Kia; Mendoza, Christopher J.; Norato, Gina; Cheung, Ken; Riekhof, Willa; Varma, Pooja; Colina-Prisco, Claudia; Emile-Backer, Magalie; Meilleur, Katherine G.; Marks, Andrew R.; Webb, Yael; Marcantonio, Eugene E.; Foley, A. Reghan; Bönnemann, Carsten G.; Mohassel, Payam
- Source
- In eClinicalMedicine February 2024 68
- Subject
- Primary Research
Articles
- Language
- ISSN
- 2589-5370