CRISPR-Cas9-mediated somatic correction of a one-base deletion in the Ugt1a gene ameliorates hyperbilirubinemia in Crigler-Najjar syndrome mice
- Resource Type
- Article
- Authors
- Bortolussi, Giulia; Iaconcig, Alessandra; Canarutto, Giulia; Porro, Fabiola; Ferrucci, Filippo; Galletta, Claudia; Díaz-Muñoz, Cristian; Rawat, Vipin; De Caneva, Alessia; Olajide, Olayemi Joseph; Zentilin, Lorena; Piazza, Silvano; Bočkor, Luka; Muro, Andrés Fernando
- Source
- In Molecular Therapy - Methods & Clinical Development 14 December 2023 31
- Subject
- Language
- ISSN
- 2329-0501