Efficient gene transduction in pigs and macaques with the engineered AAV vector AAV.GT5 for hemophilia B gene therapy
- Resource Type
- Article
- Authors
- Kashiwakura, Yuji; Endo, Kazuhiro; Ugajin, Atsushi; Kikuchi, Tomohiro; Hishikawa, Shuji; Nakamura, Hitoyasu; Katakai, Yuko; Baatartsogt, Nemekhbayar; Hiramoto, Takafumi; Hayakawa, Morisada; Kamoshita, Nobuhiko; Yamazaki, Shoji; Kume, Akihiro; Mori, Harushi; Sata, Naohiro; Sakata, Yoichi; Muramatsu, Shin-ichi; Ohmori, Tsukasa
- Source
- In Molecular Therapy - Methods & Clinical Development August 2023
- Subject
- Language
- ISSN
- 2329-0501