Effectiveness and safety of the tri-iodothyronine analogue Triac in children and adults with MCT8 deficiency: an international, single-arm, open-label, phase 2 trial
Resource Type
Article
Authors
Groeneweg, Stefan ; Peeters, Robin P ; Moran, Carla ; Stoupa, Athanasia ; Auriol, Françoise ; Tonduti, Davide ; Dica, Alice ; Paone, Laura ; Rozenkova, Klara ; Malikova, Jana ; van der Walt, Adri ; de Coo, Irenaeus F M ; McGowan, Anne ; Lyons, Greta ; Aarsen, Femke K ; Barca, Diana ; van Beynum, Ingrid M ; van der Knoop, Marieke M ; Jansen, Jurgen ; Manshande, Martien ; Lunsing, Roelineke J ; Nowak, Stan ; den Uil, Corstiaan A ; Zillikens, M Carola ; Visser, Frank E ; Vrijmoeth, Paul ; de Wit, Marie Claire Y ; Wolf, Nicole I ; Zandstra, Angelique ; Ambegaonkar, Gautam ; Singh, Yogen ; de Rijke, Yolanda B ; Medici, Marco ; Bertini, Enrico S ; Depoorter, Sylvia ; Lebl, Jan ; Cappa, Marco ; De Meirleir, Linda ; Krude, Heiko ; Craiu, Dana ; Zibordi, Federica ; Oliver Petit, Isabelle ; Polak, Michel ; Chatterjee, Krishna ; Visser, Theo J ; Visser, W Edward
Source
In The Lancet Diabetes & Endocrinology September 2019 7(9):695-706
Subject
Primary Research Articles
Language
ISSN
2213-8587