Efficacy of exon-skipping therapy for DMD cardiomyopathy with mutations in actin binding domain 1
- Resource Type
- Article
- Authors
- Shiba, Naoko; Yang, Xiao; Sato, Mitsuto; Kadota, Shin; Suzuki, Yota; Agata, Masahiro; Nagamine, Kohei; Izumi, Masaki; Honda, Yusuke; Koganehira, Tomoya; Kobayashi, Hideki; Ichimura, Hajime; Chuma, Shinichiro; Nakai, Junichi; Tohyama, Shugo; Fukuda, Keiichi; Miyazaki, Daigo; Nakamura, Akinori; Shiba, Yuji
- Source
- In Molecular Therapy - Nucleic Acids 12 December 2023 34
- Subject
- Language
- ISSN
- 2162-2531