Branch points as potential targets of exon-skipping therapies for genetic disorders
- Resource Type
- Article
- Authors
- Ohara, Hiroaki; Hosokawa, Motoyasu; Awaya, Tomonari; Hagiwara, Atsuko; Kurosawa, Ryo; Sako, Yukiya; Ogawa, Megumu; Ogasawara, Masashi; Noguchi, Satoru; Goto, Yuichi; Takahashi, Ryosuke; Nishino, Ichizo; Hagiwara, Masatoshi
- Source
- In Molecular Therapy - Nucleic Acids July 2023
- Subject
- Language
- ISSN
- 2162-2531