CRISPR-Cas9n-mediated ELANE promoter editing for gene therapy of severe congenital neutropenia
- Resource Type
- Article
- Authors
- Nasri, Masoud; Ritter, Malte U.; Mir, Perihan; Dannenmann, Benjamin; Kaufmann, Masako M.; Arreba-Tutusaus, Patricia; Xu, Yun; Borbaran-Bravo, Natalia; Klimiankou, Maksim; Lengerke, Claudia; Zeidler, Cornelia; Cathomen, Toni; Welte, Karl; Skokowa, Julia
- Source
- In Molecular Therapy March 2024
- Subject
- Language
- ISSN
- 1525-0016