Novel MeCP2 gene therapy is effective in a multicenter study using two mouse models of Rett syndrome and is safe in non-human primates
- Resource Type
- Article
- Authors
- Powers, Samantha; Likhite, Shibi; Gadalla, Kamal K.; Miranda, Carlos J.; Huffenberger, Amy J.; Dennys, Cassandra; Foust, Kevin D.; Morales, Pablo; Pierson, Christopher R.; Rinaldi, Federica; Perry, Stephanie; Bolon, Brad; Wein, Nicolas; Cobb, Stuart; Kaspar, Brian K.; Meyer, Kathrin
- Source
- In Molecular Therapy July 2023
- Subject
- Language
- ISSN
- 1525-0016