25 A phase 2/3 study evaluating the efficacy and safety of pozelimab in patients with CD55 deficiency with hyperactivation of complement, angiopathic thrombosis, and protein-losing enteropathy (CHAPLE disease)
Resource Type
Abstract
Authors
Ozen, Ahmet ; Chongsrisawat, Voranush ; Pinar Sefer, Asena ; Kolukisa, Burcu ; Jalbert, Jessica J. ; Miller, Jutta L. ; Meagher, Karoline A. ; Brackin, Taylor ; Feldman, Hagit Baris ; Adiv, Orly Eshach ; Baris, Safa ; Karakoc-Aydiner, Elif ; Eltan, Sevgi Bilgic ; Altunbaş, Melek Yorgun ; Ergelen, Rabia ; Fuss, Ivan J. ; Moorman, Heather ; Magliocco, Mary ; Matthews, Helen ; Marciano, Beatriz E. ; Suratannon, Narissara ; Chatchatee, Pantipa ; Suphapeetiporn, Kanya ; Trbovic, Caryn F. ; Burczynski, Michael E. ; Chaudhari, Umesh ; Perlee, Lorah ; Harari, Olivier A. ; Lenardo, Michael J.
Source
In Immunobiology September 2023 228(5)
Subject
Language
ISSN
0171-2985