Vector integration and fate in the hemophilia dog liver multiple years after AAV-FVIII gene transfer
- Resource Type
- Article
- Authors
- Batty, Paul; Fong, Sylvia; Franco, Matteo; Sihn, Choong-Ryoul; Swystun, Laura L.; Afzal, Saira; Harpell, Lorianne; Hurlbut, David; Pender, Abbey; Su, Cheng; Thomsen, Hauke; Wilson, Christopher; Youssar, Loubna; Winterborn, Andrew; Gil-Farina, Irene; Lillicrap, David
- Source
- In Blood February 2024
- Subject
- Gene Therapy
- Language
- ISSN
- 0006-4971