Long-Term Outcome of Gene Therapy for X-Linked Severe Combined Immunodeficiency (SCID-X1) Using an Enhancer-Deleted Self-Inactivating Gammaretroviral Vector
Resource Type
Abstract
Authors
Pai, Sung-Yun ; Nagarsheth, Nisha ; Prockop, Susan ; Armant, Myriam ; Kohn, Donald B. ; Marsh, Rebecca A. ; Booth, Claire ; Everett, John K. ; Bleesing, Jack ; Chellapandian, Deepak ; Dansereau, Colleen ; de Oliveira, Satiro ; London, Wendy B. ; Marinovic, M. Angélica ; Moore, Theodore B. ; Oleastro, Matias ; O'Toole, Grainne ; Vander Lugt, Mark ; Urdinez, Luciano ; Walkovich, Kelly J. ; Walter, Jolan E. ; Schambach, Axel ; Thrasher, Adrian J. ; Bushman, Frederic D. ; Williams, David A
Source
In Blood 15 November 2022 140 Supplement 1:10643-10645
Subject
Language
ISSN
0006-4971