Update on the safety and efficacy of retroviral gene therapy for immunodeficiency due to adenosine deaminase deficiency
- Resource Type
- Article
- Authors
- Cicalese, Maria Pia ; Ferrua, Francesca ; Castagnaro, Laura; Pajno, Roberta; Barzaghi, Federica; Giannelli, Stefania; Dionisio, Francesca; Brigida, Immacolata; Bonopane, Marco; Casiraghi, Miriam; Tabucchi, Antonella; Carlucci, Filippo; Grunebaum, Eyal; Adeli, Mehdi; Bredius, Robbert G.; Puck, Jennifer M.; Stepensky, Polina; Tezcan, Ilhan; Rolfe, Katie; De Boever, Erika; Reinhardt, Rickey R.; Appleby, Jonathan; Ciceri, Fabio; Roncarolo, Maria Grazia; Aiuti, Alessandro
- Source
- In Blood 7 July 2016 128(1):45-54
- Subject
- Language
- ISSN
- 0006-4971